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Uncovering haematopoietic system dynamics in gene therapy treated patients by retroviral tagging 1-gen-2010 Biasco, L; Baricordi, C; Merella, S; Bartholomae, C; Ambrosi, Alessandro; Pellin, D; DI SERIO, Mariaclelia; Von Kalle, C; Schmidt, M; Aiuti, Alessandro
Intensified immunosuppression with ATG reduces graft failure without affecting immune reconstitution or infections in high-risk beta thalassaemia patients after HLA-identical sibling HSCT 1-gen-2010 Biral, E; Cappelli, B; Zugna, D; Chiesa, R; Biffi, A; Zito, L; Fleischhauer, K; Bacchetta, R; Fumagalli, L; Di Serio, C; Ciceri, Fabio; Roncarolo, Mg; Aiuti, A; Marktel, S.
Uncovering Haematopoietic System Dynamics and Single Multipotent Progenitors Activity In Vivo In Humans by Retroviral Tagging 1-gen-2010 Biasco, L; Baricordi, C; Merella, S; Bartholomae, C; Ambrosi, Alessandro; Pellin, D; DI SERIO, Mariaclelia; Von Kalle, C; Schmidt, M; Aiuti, A.
TIE2-Expressing Macrophages Limit the Therapeutic Efficacy of the Vascular Disrupting Agent, Combretastatin A4 Phosphate 1-gen-2011 Welford, A. F.; Biziato, D.; Coffelt, S. B.; Nucera, S.; Fisher, M.; Pucci, F.; DI SERIO, Mariaclelia; Naldini, L.; De Palma, M.; Tozer, G. M.; Lewis, C. E.
Estimated comparative integration hotspots identify different behaviors of retroviral gene transfer vectors. 1-gen-2011 Ambrosi, Alessandro; Glad, Ik; Pellin, D; Cattoglio, C; Mavilio, F; DI SERIO, Mariaclelia; Frigessi, A.
Modelling evolution of Multiple Sclerosis: evidence from survival and longitudinal approach 1-gen-2011 DI SERIO, Mariaclelia; Zugna,
Tracking hematopoietic stem cell fate in humans by retroviral tagging 1-gen-2011 Biasco, L; Baricordi, C; Dionisio, F; Bartholomae, C; Brigida, I; Scaramuzza, S; Fronza, R; Merella, S; Ambrosi, Alessandro; Pellin, D; DI SERIO, Mariaclelia; Montini, E; Von Kalle, C; Schmidt, M; Aiuti, A.
AAV6-mediated systemic shRNA delivery reverses disease in a mouse model of facioscapulohumeral muscular dystrophy 1-gen-2011 Bortolanza, S; Nonis, A; Sanvito, F; Maciotta, S; Sitia, G; Wei, J; Torrente, Y; DI SERIO, Mariaclelia; Chamberlain, Jr; Gabellini, D.
Integration profile of retroviral vector in gene therapy treated patients is cell-specific according to gene expression and chromatin conformation of target cell 1-gen-2011 Biasco, L; Ambrosi, Alessandro; Pellin, D; Bartholomae, C; Brigida, I; Roncarolo, MARIA GRAZIA; DI SERIO, Mariaclelia; von Kalle, C; Schmidt, M; Aiuti, Alessandro
Bayesian methods for joint modeling of longitudinal and survival data to assess validity of biomarkers in AIDS data 1-gen-2012 Brombin, Chiara; Rancoita, Pmv; DI SERIO, Mariaclelia
A single-center retrospective study on 3,957 consecutive excisions of basal cell carcinomas. BCC behavior patterns: retrospective statistical analysis 1-gen-2012 Codazzi, Denis; Van Der Velden, Janneke; Carminati, Marcello; Bocchiotti, Maria Alessandra; Di Serio, Clelia; Barberis, Massimo; Robotti, Enrico
Biostatistics meets bioinformatics in integrating information from highdimensional heterogeneous genomic data: Two examples from rare genetic diseases and infectious diseases 1-gen-2012 DI SERIO, Mariaclelia; Pellin, D.; Ambrosi, Alessandro; Glad, I.; Frigessi, A.
Evaluating treatment e effect within a multivariate stochastic ordering framework: NPC methodology applied to a study on Multiple Sclerosis 1-gen-2012 Brombin, Chiara; DI SERIO, Mariaclelia
Hyperfunctional coagulation factor IX improves the efficacy of gene therapy in hemophilic mice 1-gen-2012 Cantore, A; Nair, N; Della Valle, P; Di Matteo, M; Màtrai, J; Sanvito, F; Brombin, Chiara; DI SERIO, Mariaclelia; D'Angelo, A; Chuah, M; Naldini, Luigi; Vandendriessche, T.
Modeling cancer cells growth 1-gen-2012 Brombin, Chiara; Crippa, ; DI SERIO, Mariaclelia
Tracking the Fate and Activity of Individual HSC and Memory Stem T Cell Clones in GT Patients through Insertional Tagging 1-gen-2012 Biasco, L; Baricordi, C; Cieri, N; Bartholomae, C; Calabria, A; Brigida, I; Fronza, R; Pellin, D; Di Serio, C; Montini, E; Bonini, MARIA CHIARA; von Kalle, C; Schmidt, M; Aiuti, A.
Genome-wide discovery of small RNAs in Mycobacterium tuberculosis. 1-gen-2012 Miotto, P; Forti, F; Ambrosi, Alessandro; Pellin, D; Veiga, Df; Balazsi, G; Gennaro, Ml; DI SERIO, Mariaclelia; Ghisotti, D; Cirillo, Dm
A genome-wide identification analysis of small regulatory RNAs in Mycobacterium tuberculosis by RNA-Seq and conservation analysis 1-gen-2012 Pellin, D; Miotto, P; Ambrosi, Alessandro; Cirillo, Dm; DI SERIO, Mariaclelia
Brain conditioning is instrumental for successful microglia reconstitution following hematopoietic stem cell transplantation 1-gen-2012 Capotondo, A; Milazzo, R; Politi, Ls; Quattrini, A; Palini, A; Plati, T; Merella, S; Nonis, A; DI SERIO, Mariaclelia; Montini, E; Naldini, Luigi; Biffi, A.
In vivo mouse models for vector genotoxicity testing and lentiviral vector-based cancer gene discovery 1-gen-2012 Cesana, Daniela; Volpin, Monica; Ranzani, Marco; Bartholomae, Cynthia; Merella, Stefania; Benedicenti, Fabrizio; Sergi Lucia, Sergi; Sanvito, Francesca; Brombin, Chiara; Nonis, Alessandro; DI SERIO, Mariaclelia; Doglioni, Claudio; Vonkalle, Christof; Schmidt, Manfred; Naldini, Luigi; Montini, Eugenio
Mostrati risultati da 41 a 60 di 135
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