Sfoglia per Autore
Epigenome-editing strategies to enhance oligodendroglial differentiation from human induced pluripotent stem cells
2022-01-01 Luciani, M; Garsia, C; Ciccarelli, E; Migliara, A; Lombardo, A; Gritti, A
Investigating the role of innate immune signaling in cell toxicity upon AAV-mediated gene transfer in hiPSC-derived CNS model
2022-01-01 Costa Verdera, H; Abou Alezz, M; Meneghini, V; Mangiameli, E; Cavalca, E; Ditadi, A; Giordano, Ms; Singh, I; Kuranda, K; Gritti, A; Merelli, I; Mingozzi, F; Kajaste-Rudnitski, A
Improving gene therapy approaches for globoid cell leukodystrophy: pre-clinical testing of chimeric GALC enzymes with enhanced bioavailability in human neural and hematopoietic cells
2022-01-01 Ricca, A; Freschi, M; Valeri, E; Unali, G; Cascino, F; Morena, F; Martino, S; Kajaste-Rudnitski, A; Gritti, A
Exploring the identity and safety of hiPSC-derived neural stem/progenitor cells: implications for cell therapy approaches
2022-01-01 Luciani, M; Meneghini, Vasco; Garsia, C; Petiti, L; Cifola, I; Beretta, S; Merelli, I; Peano, C; Miccio, A; Gritti, A
An innovative platform approach for the development of ex-vivo gene therapies for the treatment of lysosomal storage diseases with skeletal involvement
2022-01-01 Forni, C; Gabaldo, M; Crippa, S; Scala, S; Consiglieri, G; Tucci, F; Passerini, L; Gritti, A; Gregori, S; Ferrari, G; Albertini, P; Galimberti, Mg; Valsecchi, A; Corti, A; Zancan, S Scarpa M; Parini, R; Naldini, L; Gentner, B; Bernardo, Me; Aiuti, A
Generation of neuronal/glial mixed cultures from human induced pluripotent stem cells (hiPSCs)
2022-01-01 Mangiameli, E.; Freschi, M.; Luciani, M.; Gritti, A.
Isolation and Culture of Neural Stem/Progenitor Cells from the Postnatal Periventricular Region
2022-01-01 Ricca, A.; Cascino, F.; Gritti, A.
Therapeutic advantages of combined gene/cell therapy strategies in a murine model of {GM}2 gangliosidosis
2022-01-01 Sala, Davide; Ornaghi, Francesca; Morena, Francesco; Argentati, Chiara; Valsecchi, Manuela; Alberizzi, Valeria; Di Guardo, Roberta; Bolino, Alessandra; Aureli, Massimo; Martino, Sabata; Gritti, Angela
In vivo Gene Therapy to the Liver and Nervous System: Promises and Challenges
2022-01-01 Cantore, Alessio; Fraldi, Alessandro; Meneghini, Vasco; Gritti, Angela
DNA damage contributes to neurotoxic inflammation in Aicardi-Goutières syndrome astrocytes
2022-01-01 Giordano, Anna Maria Sole; Luciani, Marco; Gatto, Francesca; Abou Alezz, Monah; Beghè, Chiara; Della Volpe, Lucrezia; Migliara, Alessandro; Valsoni, Sara; Genua, Marco; Dzieciatkowska, Monika; Frati, Giacomo; Tahraoui-Bories, Julie; Giliani, Silvia Clara; Orcesi, Simona; Fazzi, Elisa; Ostuni, Renato; D'Alessandro, Angelo; Di Micco, Raffaella; Merelli, Ivan; Lombardo, Angelo; Reijns, Martin A M; Gromak, Natalia; Gritti, Angela; Kajaste-Rudnitski, Anna
Human iPSC-derived neural stem cells display a radial glia-like signaturein vitroand favorable long-term safety in transplanted mice
2023-08-04 Luciani, Marco; Garsia, Chiara; Beretta, Stefano; Petiti, Luca; Peano, Clelia; Merelli, Ivan; Cifola, Ingrid; Miccio, Annarita; Meneghini, Vasco; Gritti, Angela
Titolo | Data di pubblicazione | Autore(i) | File |
---|---|---|---|
Epigenome-editing strategies to enhance oligodendroglial differentiation from human induced pluripotent stem cells | 1-gen-2022 | Luciani, M; Garsia, C; Ciccarelli, E; Migliara, A; Lombardo, A; Gritti, A | |
Investigating the role of innate immune signaling in cell toxicity upon AAV-mediated gene transfer in hiPSC-derived CNS model | 1-gen-2022 | Costa Verdera, H; Abou Alezz, M; Meneghini, V; Mangiameli, E; Cavalca, E; Ditadi, A; Giordano, Ms; Singh, I; Kuranda, K; Gritti, A; Merelli, I; Mingozzi, F; Kajaste-Rudnitski, A | |
Improving gene therapy approaches for globoid cell leukodystrophy: pre-clinical testing of chimeric GALC enzymes with enhanced bioavailability in human neural and hematopoietic cells | 1-gen-2022 | Ricca, A; Freschi, M; Valeri, E; Unali, G; Cascino, F; Morena, F; Martino, S; Kajaste-Rudnitski, A; Gritti, A | |
Exploring the identity and safety of hiPSC-derived neural stem/progenitor cells: implications for cell therapy approaches | 1-gen-2022 | Luciani, M; Meneghini, Vasco; Garsia, C; Petiti, L; Cifola, I; Beretta, S; Merelli, I; Peano, C; Miccio, A; Gritti, A | |
An innovative platform approach for the development of ex-vivo gene therapies for the treatment of lysosomal storage diseases with skeletal involvement | 1-gen-2022 | Forni, C; Gabaldo, M; Crippa, S; Scala, S; Consiglieri, G; Tucci, F; Passerini, L; Gritti, A; Gregori, S; Ferrari, G; Albertini, P; Galimberti, Mg; Valsecchi, A; Corti, A; Zancan, S Scarpa M; Parini, R; Naldini, L; Gentner, B; Bernardo, Me; Aiuti, A | |
Generation of neuronal/glial mixed cultures from human induced pluripotent stem cells (hiPSCs) | 1-gen-2022 | Mangiameli, E.; Freschi, M.; Luciani, M.; Gritti, A. | |
Isolation and Culture of Neural Stem/Progenitor Cells from the Postnatal Periventricular Region | 1-gen-2022 | Ricca, A.; Cascino, F.; Gritti, A. | |
Therapeutic advantages of combined gene/cell therapy strategies in a murine model of {GM}2 gangliosidosis | 1-gen-2022 | Sala, Davide; Ornaghi, Francesca; Morena, Francesco; Argentati, Chiara; Valsecchi, Manuela; Alberizzi, Valeria; Di Guardo, Roberta; Bolino, Alessandra; Aureli, Massimo; Martino, Sabata; Gritti, Angela | |
In vivo Gene Therapy to the Liver and Nervous System: Promises and Challenges | 1-gen-2022 | Cantore, Alessio; Fraldi, Alessandro; Meneghini, Vasco; Gritti, Angela | |
DNA damage contributes to neurotoxic inflammation in Aicardi-Goutières syndrome astrocytes | 1-gen-2022 | Giordano, Anna Maria Sole; Luciani, Marco; Gatto, Francesca; Abou Alezz, Monah; Beghè, Chiara; Della Volpe, Lucrezia; Migliara, Alessandro; Valsoni, Sara; Genua, Marco; Dzieciatkowska, Monika; Frati, Giacomo; Tahraoui-Bories, Julie; Giliani, Silvia Clara; Orcesi, Simona; Fazzi, Elisa; Ostuni, Renato; D'Alessandro, Angelo; Di Micco, Raffaella; Merelli, Ivan; Lombardo, Angelo; Reijns, Martin A M; Gromak, Natalia; Gritti, Angela; Kajaste-Rudnitski, Anna | |
Human iPSC-derived neural stem cells display a radial glia-like signaturein vitroand favorable long-term safety in transplanted mice | 4-ago-2023 | Luciani, Marco; Garsia, Chiara; Beretta, Stefano; Petiti, Luca; Peano, Clelia; Merelli, Ivan; Cifola, Ingrid; Miccio, Annarita; Meneghini, Vasco; Gritti, Angela |
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