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Mostrati risultati da 17.203 a 17.222 di 47.107
Titolo Data di pubblicazione Autore(i) File
Gene Therapy Approaches to Hemoglobinopathies 1-gen-2017 Ferrari, Giuliana; Cavazzana, Marina; Mavilio, Fulvio
Gene therapy augments the efficacy of hematopoietic cell transplantation and fully corrects mucopolysaccharidosis type I phenotype in the mouse model 1-gen-2010 Visigalli, I; Delai, S; Politi, Ls; Di Domenico, C; Cerri, F; Mrak, E; D'Isa, R; Ungaro, D; Stok, M; Sanvito, F; Mariani, E; Staszewsky, L; Godi, C; Russo, I; Cecere, F; Del Carro, U; Rubinacci, A; Brambilla, R; Quattrini, A; Di Natale, P; Ponder, K; Naldini, Luigi; Biffi, A.
Gene therapy clinical trials for relapsed leukemia with infusions of the suicide-gene transduced donor lymphocytes in Japan 1-gen-2006 Onodera, M; Kaneko, S; Otsu, M; Okoshi, Y; Kojima, H; Shimizu, T; Fukushima, T; Sumazaki, R; Bonini, MARIA CHIARA; Bordignon, Claudio; Nakauchi, H; Nagasawa, T.
Gene therapy for a mucopolysaccharidosis type I murine model with lentiviral-IDUA vector 1-gen-2005 Di Domenico, C; Villani, Grd; Di Napoli, D; Reyero, Egy; Lombardo, ANGELO LEONE; Naldini, Luigi; Di Natale, P.
Gene therapy for ADA-SCID, the first marketing approval of an ex vivo gene therapy in Europe: paving the road for the next generation of advanced therapy medicinal products 1-gen-2017 Aiuti, Alessandro; Roncarolo, MARIA GRAZIA; Naldini, Luigi
Gene therapy for adenosine deaminase deficiency 1-gen-2003 Aiuti, A; Ficara, F; Cattaneo, F; Bordignon, Claudio; Roncarolo, MARIA GRAZIA
Gene Therapy for Adenosine Deaminase Deficiency 1-gen-2010 Cappelli, B; Aiuti, Alessandro
Gene Therapy for Adenosine Deaminase Deficiency: A Comprehensive Evaluation of Short- and Medium-Term Safety 1-gen-2018 Cicalese, Maria Pia; Ferrua, Francesca; Castagnaro, Laura; Rolfe, Katie; De Boever, Erika; Reinhardt, Rickey R.; Appleby, Jonathan; Roncarolo, Maria Grazia; Aiuti, Alessandro
Gene therapy for adenosine-deaminase-deficient severe combined immunodeficiency 1-gen-2004 Aiuti, Alessandro
Gene therapy for autoimmune diseases 1-gen-2004 Furlan, R; Butti, E; Pluchino, S; Martino, Gianvito
Gene therapy for beta thalassemia: preclinical studies on human cells 1-gen-2006 Roselli, Ea; Cesari, R; Miccio, A; Tiboni, F; Corbella, P; Rossi, C; Biral, E; Marktel, S; Antoniou, M; Andreani, M; Lucarelli, G; Ferrari, Giuliana
Gene therapy for beta-thalassemia: analysis of therapeutic efficiency in pre-clinical models 1-gen-2008 Roselli, E; Miccio, A; Rossi, C; Tiboni, F; Marktel, S; Biral, E; Sanvito, F; Ponzoni, M; Andreani, M; Ferrari, Giuliana; Lucarelli, G.
Gene therapy for beta-thalassemia: Preclinical studies on human cells. 1-gen-2006 Ferrari, Giuliana; Roselli, E; Tiboni, F; Biral, E; Marktel, S; Antoniou, M; Andreani, M; Lucarelli, G; Cesari, R; Miccio, A.
Gene therapy for congenital diseases 1-gen-1991 Rossini, S.; Bordignon, Claudio
Gene Therapy for Hemoglobinopathies 1-gen-2023 Lidonnici, Maria Rosa; Scaramuzza, Samantha; Ferrari, Giuliana
Gene therapy for immunodeficiency due to adenosine deaminase deficiency 1-gen-2009 Aiuti, Alessandro; Cattaneo, F; Galimberti, S; Benninghoff, U; Cassani, B; Callegaro, L; Scaramuzza, S; Andolfi, G; Mirolo, M; Brigida, I; Tabucchi, A; Carlucci, F; Eibl, M; Aker, M; Slavin, S; AL MOUSA, H; AL GHONAIUM, A; Ferster, A; Duppenthaler, A; Notarangelo, L; Wintergerst, U; Buckley, R. H.; Bregni, M; Marktel, S; Valsecchi, M. G.; Rossi, P; Ciceri, Fabio; Miniero, R; Bordignon, Claudio; Roncarolo, MARIA GRAZIA
Gene therapy for leukemia: alloreactivity and beyond 1-gen-2009 Bonini, MARIA CHIARA
Gene therapy for lysosomal storage disorders 1-gen-2011 Gritti, A.
Gene therapy for lysosomal storage disorders: recent advances for metachromatic leukodystrophy and mucopolysaccaridosis I 1-gen-2017 Penati, Rachele; Fumagalli, Francesca; Calbi, Valeria; Bernardo, Maria Ester; Aiuti, Alessandro
Gene therapy for mucopolysaccharidoses: In vivo and ex vivo approaches 10 Technology 1004 Medical Biotechnology 1-gen-2018 Fraldi, A.; Serafini, M.; Sorrentino, N. C.; Gentner, B.; Aiuti, A.; Bernardo, M. E.
Mostrati risultati da 17.203 a 17.222 di 47.107
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