Sfoglia per Titolo
Gene therapy approaches for autoimmune diseases of central nervous system and other tissues
2005-01-01 Furlan, R; Butti, E; Pluchino, S; Martino, Gianvito
Gene Therapy Approaches to Hemoglobinopathies
2017-01-01 Ferrari, Giuliana; Cavazzana, Marina; Mavilio, Fulvio
Gene therapy augments the efficacy of hematopoietic cell transplantation and fully corrects mucopolysaccharidosis type I phenotype in the mouse model
2010-01-01 Visigalli, I; Delai, S; Politi, Ls; Di Domenico, C; Cerri, F; Mrak, E; D'Isa, R; Ungaro, D; Stok, M; Sanvito, F; Mariani, E; Staszewsky, L; Godi, C; Russo, I; Cecere, F; Del Carro, U; Rubinacci, A; Brambilla, R; Quattrini, A; Di Natale, P; Ponder, K; Naldini, Luigi; Biffi, A.
Gene therapy clinical trials for relapsed leukemia with infusions of the suicide-gene transduced donor lymphocytes in Japan
2006-01-01 Onodera, M; Kaneko, S; Otsu, M; Okoshi, Y; Kojima, H; Shimizu, T; Fukushima, T; Sumazaki, R; Bonini, MARIA CHIARA; Bordignon, Claudio; Nakauchi, H; Nagasawa, T.
Gene therapy for a mucopolysaccharidosis type I murine model with lentiviral-IDUA vector
2005-01-01 Di Domenico, C; Villani, Grd; Di Napoli, D; Reyero, Egy; Lombardo, ANGELO LEONE; Naldini, Luigi; Di Natale, P.
Gene therapy for ADA-SCID, the first marketing approval of an ex vivo gene therapy in Europe: paving the road for the next generation of advanced therapy medicinal products
2017-01-01 Aiuti, Alessandro; Roncarolo, MARIA GRAZIA; Naldini, Luigi
Gene therapy for adenosine deaminase deficiency
2003-01-01 Aiuti, A; Ficara, F; Cattaneo, F; Bordignon, Claudio; Roncarolo, MARIA GRAZIA
Gene Therapy for Adenosine Deaminase Deficiency
2010-01-01 Cappelli, B; Aiuti, Alessandro
Gene Therapy for Adenosine Deaminase Deficiency: A Comprehensive Evaluation of Short- and Medium-Term Safety
2018-01-01 Cicalese, Maria Pia; Ferrua, Francesca; Castagnaro, Laura; Rolfe, Katie; De Boever, Erika; Reinhardt, Rickey R.; Appleby, Jonathan; Roncarolo, Maria Grazia; Aiuti, Alessandro
Gene therapy for adenosine-deaminase-deficient severe combined immunodeficiency
2004-01-01 Aiuti, Alessandro
Gene therapy for autoimmune diseases
2004-01-01 Furlan, R; Butti, E; Pluchino, S; Martino, Gianvito
Gene therapy for beta thalassemia: preclinical studies on human cells
2006-01-01 Roselli, Ea; Cesari, R; Miccio, A; Tiboni, F; Corbella, P; Rossi, C; Biral, E; Marktel, S; Antoniou, M; Andreani, M; Lucarelli, G; Ferrari, Giuliana
Gene therapy for beta-thalassemia: analysis of therapeutic efficiency in pre-clinical models
2008-01-01 Roselli, E; Miccio, A; Rossi, C; Tiboni, F; Marktel, S; Biral, E; Sanvito, F; Ponzoni, M; Andreani, M; Ferrari, Giuliana; Lucarelli, G.
Gene therapy for beta-thalassemia: Preclinical studies on human cells.
2006-01-01 Ferrari, Giuliana; Roselli, E; Tiboni, F; Biral, E; Marktel, S; Antoniou, M; Andreani, M; Lucarelli, G; Cesari, R; Miccio, A.
Gene therapy for congenital diseases
1991-01-01 Rossini, S.; Bordignon, Claudio
Gene therapy for immunodeficiency due to adenosine deaminase deficiency
2009-01-01 Aiuti, Alessandro; Cattaneo, F; Galimberti, S; Benninghoff, U; Cassani, B; Callegaro, L; Scaramuzza, S; Andolfi, G; Mirolo, M; Brigida, I; Tabucchi, A; Carlucci, F; Eibl, M; Aker, M; Slavin, S; AL MOUSA, H; AL GHONAIUM, A; Ferster, A; Duppenthaler, A; Notarangelo, L; Wintergerst, U; Buckley, R. H.; Bregni, M; Marktel, S; Valsecchi, M. G.; Rossi, P; Ciceri, Fabio; Miniero, R; Bordignon, Claudio; Roncarolo, MARIA GRAZIA
Gene therapy for leukemia: alloreactivity and beyond
2009-01-01 Bonini, MARIA CHIARA
Gene therapy for lysosomal storage disorders: recent advances for metachromatic leukodystrophy and mucopolysaccaridosis I
2017-01-01 Penati, Rachele; Fumagalli, Francesca; Calbi, Valeria; Bernardo, Maria Ester; Aiuti, Alessandro
Gene therapy for mucopolysaccharidoses: In vivo and ex vivo approaches 10 Technology 1004 Medical Biotechnology
2018-01-01 Fraldi, A.; Serafini, M.; Sorrentino, N. C.; Gentner, B.; Aiuti, A.; Bernardo, M. E.
Gene therapy for primary immunodeficiencies: Part 1
2012-01-01 Cavazzana Calvo, M; Fischer, A; Hacein Bey Abina, S; Aiuti, Alessandro
Titolo | Data di pubblicazione | Autore(i) | File |
---|---|---|---|
Gene therapy approaches for autoimmune diseases of central nervous system and other tissues | 1-gen-2005 | Furlan, R; Butti, E; Pluchino, S; Martino, Gianvito | |
Gene Therapy Approaches to Hemoglobinopathies | 1-gen-2017 | Ferrari, Giuliana; Cavazzana, Marina; Mavilio, Fulvio | |
Gene therapy augments the efficacy of hematopoietic cell transplantation and fully corrects mucopolysaccharidosis type I phenotype in the mouse model | 1-gen-2010 | Visigalli, I; Delai, S; Politi, Ls; Di Domenico, C; Cerri, F; Mrak, E; D'Isa, R; Ungaro, D; Stok, M; Sanvito, F; Mariani, E; Staszewsky, L; Godi, C; Russo, I; Cecere, F; Del Carro, U; Rubinacci, A; Brambilla, R; Quattrini, A; Di Natale, P; Ponder, K; Naldini, Luigi; Biffi, A. | |
Gene therapy clinical trials for relapsed leukemia with infusions of the suicide-gene transduced donor lymphocytes in Japan | 1-gen-2006 | Onodera, M; Kaneko, S; Otsu, M; Okoshi, Y; Kojima, H; Shimizu, T; Fukushima, T; Sumazaki, R; Bonini, MARIA CHIARA; Bordignon, Claudio; Nakauchi, H; Nagasawa, T. | |
Gene therapy for a mucopolysaccharidosis type I murine model with lentiviral-IDUA vector | 1-gen-2005 | Di Domenico, C; Villani, Grd; Di Napoli, D; Reyero, Egy; Lombardo, ANGELO LEONE; Naldini, Luigi; Di Natale, P. | |
Gene therapy for ADA-SCID, the first marketing approval of an ex vivo gene therapy in Europe: paving the road for the next generation of advanced therapy medicinal products | 1-gen-2017 | Aiuti, Alessandro; Roncarolo, MARIA GRAZIA; Naldini, Luigi | |
Gene therapy for adenosine deaminase deficiency | 1-gen-2003 | Aiuti, A; Ficara, F; Cattaneo, F; Bordignon, Claudio; Roncarolo, MARIA GRAZIA | |
Gene Therapy for Adenosine Deaminase Deficiency | 1-gen-2010 | Cappelli, B; Aiuti, Alessandro | |
Gene Therapy for Adenosine Deaminase Deficiency: A Comprehensive Evaluation of Short- and Medium-Term Safety | 1-gen-2018 | Cicalese, Maria Pia; Ferrua, Francesca; Castagnaro, Laura; Rolfe, Katie; De Boever, Erika; Reinhardt, Rickey R.; Appleby, Jonathan; Roncarolo, Maria Grazia; Aiuti, Alessandro | |
Gene therapy for adenosine-deaminase-deficient severe combined immunodeficiency | 1-gen-2004 | Aiuti, Alessandro | |
Gene therapy for autoimmune diseases | 1-gen-2004 | Furlan, R; Butti, E; Pluchino, S; Martino, Gianvito | |
Gene therapy for beta thalassemia: preclinical studies on human cells | 1-gen-2006 | Roselli, Ea; Cesari, R; Miccio, A; Tiboni, F; Corbella, P; Rossi, C; Biral, E; Marktel, S; Antoniou, M; Andreani, M; Lucarelli, G; Ferrari, Giuliana | |
Gene therapy for beta-thalassemia: analysis of therapeutic efficiency in pre-clinical models | 1-gen-2008 | Roselli, E; Miccio, A; Rossi, C; Tiboni, F; Marktel, S; Biral, E; Sanvito, F; Ponzoni, M; Andreani, M; Ferrari, Giuliana; Lucarelli, G. | |
Gene therapy for beta-thalassemia: Preclinical studies on human cells. | 1-gen-2006 | Ferrari, Giuliana; Roselli, E; Tiboni, F; Biral, E; Marktel, S; Antoniou, M; Andreani, M; Lucarelli, G; Cesari, R; Miccio, A. | |
Gene therapy for congenital diseases | 1-gen-1991 | Rossini, S.; Bordignon, Claudio | |
Gene therapy for immunodeficiency due to adenosine deaminase deficiency | 1-gen-2009 | Aiuti, Alessandro; Cattaneo, F; Galimberti, S; Benninghoff, U; Cassani, B; Callegaro, L; Scaramuzza, S; Andolfi, G; Mirolo, M; Brigida, I; Tabucchi, A; Carlucci, F; Eibl, M; Aker, M; Slavin, S; AL MOUSA, H; AL GHONAIUM, A; Ferster, A; Duppenthaler, A; Notarangelo, L; Wintergerst, U; Buckley, R. H.; Bregni, M; Marktel, S; Valsecchi, M. G.; Rossi, P; Ciceri, Fabio; Miniero, R; Bordignon, Claudio; Roncarolo, MARIA GRAZIA | |
Gene therapy for leukemia: alloreactivity and beyond | 1-gen-2009 | Bonini, MARIA CHIARA | |
Gene therapy for lysosomal storage disorders: recent advances for metachromatic leukodystrophy and mucopolysaccaridosis I | 1-gen-2017 | Penati, Rachele; Fumagalli, Francesca; Calbi, Valeria; Bernardo, Maria Ester; Aiuti, Alessandro | |
Gene therapy for mucopolysaccharidoses: In vivo and ex vivo approaches 10 Technology 1004 Medical Biotechnology | 1-gen-2018 | Fraldi, A.; Serafini, M.; Sorrentino, N. C.; Gentner, B.; Aiuti, A.; Bernardo, M. E. | |
Gene therapy for primary immunodeficiencies: Part 1 | 1-gen-2012 | Cavazzana Calvo, M; Fischer, A; Hacein Bey Abina, S; Aiuti, Alessandro |
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