Sfoglia per Rivista EMBO MOLECULAR MEDICINE
A serum circulating miRNA diagnostic test to identify asymptomatic high-risk individuals with early stage lung cancer
2011-01-01 Bianchi, F; Nicassio, F; Marzi, M; Belloni, E; Dall'Olio, V; Bernard, L; Pelosi, G; Maisonneuve, P; Veronesi, G; Di Fiore, Pp
Coenzyme A corrects pathological defects in human neurons of PANK2-associated neurodegeneration
2016-01-01 Orellana, Daniel I; Santambrogio, Paolo; Rubio, Alicia; Yekhlef, Latefa; Cancellieri, Cinzia; Dusi, Sabrina; Giannelli, Serena G; Venco, Paola; Mazzara, Pietro G; Cozzi, Anna; Ferrari, Maurizio; Garavaglia, Barbara; Taverna, Stefano; Tiranti, Valeria; Broccoli, Vania; Levi, SONIA MARIA ROSA
Correction of ß-thalassemia major by gene transfer in hematopoietic progenitors of pediatric patients
2010-01-01 Roselli, Ea; Mezzadra, R; Frittoli, Mc; Maruggi, G; Biral, E; Mavilio, F; Mastropietro, F; Amato, A; Tonon, G; Refaldi, C; Cappellini, Md; Andreani, M; Lucarelli, G; Roncarolo, MARIA GRAZIA; Marktel, S; Ferrari, Giuliana
CXCR4 engagement triggers CD47 internalization and antitumor immunization in a mouse model of mesothelioma
2021-01-01 Mezzapelle, R.; De Marchis, F.; Passera, C.; Leo, M.; Brambilla, F.; Colombo, F.; Casalgrandi, M.; Preti, A.; Zambrano, S.; Castellani, P.; Ertassi, R.; Silingardi, M.; Caprioglio, F.; Basso, V.; Boldorini, R.; Carretta, A.; Sanvito, F.; Rena, O.; Rubartelli, A.; Sabatino, L.; Mondino, A.; Crippa, M. P.; Colantuoni, V.; Bianchi, M. E.
Defective glutamate and K+ clearance by cortical astrocytes in familial hemiplegic migraine type 2
2016-01-01 Capuani, Clizia; Melone, Marcello; Tottene, Angelita; Bragina, Luca; Crivellaro, Giovanna; Santello, Mirko; Casari, GIORGIO NEVIO; Conti, Fiorenzo; Pietrobon, Daniela
Gene therapy for ADA-SCID, the first marketing approval of an ex vivo gene therapy in Europe: paving the road for the next generation of advanced therapy medicinal products
2017-01-01 Aiuti, Alessandro; Roncarolo, MARIA GRAZIA; Naldini, Luigi
Genetic engineering of hematopoiesis: current stage of clinical translation and future perspectives
2019-01-01 Naldini, Luigi
HIF factors cooperate with PML-RARα to promote acute promyelocytic leukemia progression and relapse
2014-01-01 Coltella, N; Percio, S; Valsecchi, R; Cuttano, R; Guarnerio, J; Ponzoni, Maurilio; Pandolfi, Pp; Melillo, G; Pattini, L; Bernardi, R.
IFN gene/cell therapy curbs colorectal cancer colonization of the liver by acting on the hepatic microenvironment
2016-01-01 Catarinella, Mario; Monestiroli, Andrea; Escobar, Giulia; Fiocchi, Amleto; Tran, Ngoc Lan; Aiolfi, Roberto; Marra, Paolo; Esposito, Antonio; Cipriani, Federica; Aldrighetti, Luca; Iannacone, Matteo; Naldini, Luigi; Guidotti, Luca G.; Sitia, Giovanni
Integration profile of retroviral vector in gene therapy treated patients is cell-specific according to gene expression and chromatin conformation of target cell
2011-01-01 Biasco, L; Ambrosi, Alessandro; Pellin, D; Bartholomae, C; Brigida, I; Roncarolo, MARIA GRAZIA; DI SERIO, Mariaclelia; von Kalle, C; Schmidt, M; Aiuti, Alessandro
Intra-arterial transplantation of HLA-matched donor mesoangioblasts in Duchenne muscular dystrophy
2015-01-01 Cossu, G; Previtali, Sc; Napolitano, S; Cicalese, Mp; Tedesco, Fs; Nicastro, F; Noviello, M; Roostalu, U; Natali Sora, Mg; Scarlato, M; De Pellegrin, M; Godi, C; Giuliani, S; Ciotti, F; Tonlorenzi, R; Lorenzetti, I; Rivellini, C; Benedetti, S; Gatti, R; Marktel, S; Mazzi, B; Tettamanti, A; Ragazzi, M; Imro, Ma; Marano, G; Ambrosi, Alessandro; Fiori, R; Sormani, Mp; Bonini, MARIA CHIARA; Venturini, M; Politi, Ls; Torrente, Y; Ciceri, Fabio
Lentiviral vectors escape innate sensing but trigger p53 in human hematopoietic stem and progenitor cells
2017-01-01 Piras, Francesco; Riba, Michela; Petrillo, Carolina; Lazarevic, Dejan; Cuccovillo, Ivan; Bartolaccini, Sara; Stupka, Elia; Gentner, Bernhard; Cittaro, Davide; Naldini, Luigi; Kajaste rudnitski, Anna
Liver gene therapy by lentiviral vectors reverses anti-factor IX pre-existing immunity in haemophilic mice
2013-01-01 Annoni, A; Cantore, A; Della Valle, P; Goudy, K; Akbarpour, M; Russo, F; Bartolaccini, S; D'Angelo, A; Roncarolo, MARIA GRAZIA; Naldini, Luigi
Maternally inherited genetic variants of CADPS2 are present in Autism Spectrum Disorders and Intellectual Disability patients
2014-01-01 Bonora, E; Graziano, C; Minopoli, F; Bacchelli, E; Magini, P; Diquigiovanni, C; Lomartire, S; Bianco, F; Vargiolu, M; Parchi, P; Marasco, E; Mantovani, V; Rampoldi, L; Trudu, M; Parmeggiani, A; Battaglia, A; Mazzone, L; Tortora, G; Maestrini, E; Seri, M; Romeo, G
Modeling, optimization, and comparable efficacy of T cell and hematopoietic stem cell gene editing for treating hyper-IgM syndrome
2021-01-01 Vavassori, V.; Mercuri, E.; Marcovecchio, G. E.; Castiello, M. C.; Schiroli, G.; Albano, L.; Margulies, C.; Buquicchio, F.; Fontana, E.; Beretta, S.; Merelli, I.; Cappelleri, A.; Rancoita, P. M. V.; Lougaris, V.; Plebani, A.; Kanariou, M.; Lankester, A.; Ferrua, F.; Scanziani, E.; Cotta-Ramusino, C.; Villa, A.; Naldini, L.; Genovese, P.
Pathogen-specific B-cell receptors drive chronic lymphocytic leukemia by light-chain-dependent cross-reaction with autoantigens
2017-01-01 Jiménez de Oya, Nereida; De Giovanni, Marco; Fioravanti, Jessica; Übelhart, Rudolf; Di Lucia, Pietro; Fiocchi, Amleto; Iacovelli, Stefano; Efremov, Dimitar G; Caligaris-Cappio, Federico; Jumaa, Hassan; Ghia, Paolo; Guidotti, Luca G; Iannacone, Matteo
Pervasive supply of therapeutic lysosomal enzymes in the CNS of normal and Krabbe-affected non-human primates by intracerebral lentiviral gene therapy
2016-01-01 Meneghini, Vasco; Lattanzi, Annalisa; Tiradani, Luigi; Bravo, Gabriele; Morena, Francesco; Sanvito, Francesca; Calabria, Andrea; Bringas, John; Fisher-Perkins, Jeanne M; Dufour, Jason P; Baker, Kate C; Doglioni, Claudio; Montini, Eugenio; Bunnell, Bruce A; Bankiewicz, Krystof; Martino, Sabata; Naldini, Luigi; Gritti, Angela
Pharmacological or genetic inhibition of iNOS prevents cachexia-mediated muscle wasting and its associated metabolism defects
2021-01-01 Sadek, J.; Hall, D. T.; Colalillo, B.; Omer, A.; Tremblay, A. -M. K.; Sanguin-Gendreau, V.; Muller, W.; Di Marco, S.; Bianchi, M. E.; Gallouzi, I. -E.
Reversible immortalisation enables genetic correction of human muscle progenitors and engineering of next-generation human artificial chromosomes for Duchenne muscular dystrophy
2018-01-01 Benedetti, Sara; Uno, Narumi; Hoshiya, Hidetoshi; Ragazzi, Martina; Ferrari, Giuliana; Kazuki, Yasuhiro; Moyle, Louise Anne; Tonlorenzi, Rossana; Lombardo, Angelo; Chaouch, Soraya; Mouly, Vincent; Moore, Marc; Popplewell, Linda; Kazuki, Kanako; Katoh, Motonobu; Naldini, Luigi; Dickson, George; Messina, Graziella; Oshimura, Mitsuo; Cossu, Giulio; Tedesco, Francesco Saverio
Targeted gene therapy and cell reprogramming in Fanconi anemia
2014-01-01 Rio, P; Baños, R; Lombardo, ANGELO LEONE; Quintana Bustamante, O; Alvarez, L; Garate, Z; Genovese, P; Almarza, E; Valeri, A; Díez, B; Navarro, S; Torres, Y; Trujillo, Jp; Murillas, R; Segovia, Jc; Samper, E; Surralles, J; Gregory, Pd; Holmes, Mc; Naldini, Luigi; Bueren, Ja
| Titolo | Data di pubblicazione | Autore(i) | File |
|---|---|---|---|
| A serum circulating miRNA diagnostic test to identify asymptomatic high-risk individuals with early stage lung cancer | 1-gen-2011 | Bianchi, F; Nicassio, F; Marzi, M; Belloni, E; Dall'Olio, V; Bernard, L; Pelosi, G; Maisonneuve, P; Veronesi, G; Di Fiore, Pp | |
| Coenzyme A corrects pathological defects in human neurons of PANK2-associated neurodegeneration | 1-gen-2016 | Orellana, Daniel I; Santambrogio, Paolo; Rubio, Alicia; Yekhlef, Latefa; Cancellieri, Cinzia; Dusi, Sabrina; Giannelli, Serena G; Venco, Paola; Mazzara, Pietro G; Cozzi, Anna; Ferrari, Maurizio; Garavaglia, Barbara; Taverna, Stefano; Tiranti, Valeria; Broccoli, Vania; Levi, SONIA MARIA ROSA | |
| Correction of ß-thalassemia major by gene transfer in hematopoietic progenitors of pediatric patients | 1-gen-2010 | Roselli, Ea; Mezzadra, R; Frittoli, Mc; Maruggi, G; Biral, E; Mavilio, F; Mastropietro, F; Amato, A; Tonon, G; Refaldi, C; Cappellini, Md; Andreani, M; Lucarelli, G; Roncarolo, MARIA GRAZIA; Marktel, S; Ferrari, Giuliana | |
| CXCR4 engagement triggers CD47 internalization and antitumor immunization in a mouse model of mesothelioma | 1-gen-2021 | Mezzapelle, R.; De Marchis, F.; Passera, C.; Leo, M.; Brambilla, F.; Colombo, F.; Casalgrandi, M.; Preti, A.; Zambrano, S.; Castellani, P.; Ertassi, R.; Silingardi, M.; Caprioglio, F.; Basso, V.; Boldorini, R.; Carretta, A.; Sanvito, F.; Rena, O.; Rubartelli, A.; Sabatino, L.; Mondino, A.; Crippa, M. P.; Colantuoni, V.; Bianchi, M. E. | |
| Defective glutamate and K+ clearance by cortical astrocytes in familial hemiplegic migraine type 2 | 1-gen-2016 | Capuani, Clizia; Melone, Marcello; Tottene, Angelita; Bragina, Luca; Crivellaro, Giovanna; Santello, Mirko; Casari, GIORGIO NEVIO; Conti, Fiorenzo; Pietrobon, Daniela | |
| Gene therapy for ADA-SCID, the first marketing approval of an ex vivo gene therapy in Europe: paving the road for the next generation of advanced therapy medicinal products | 1-gen-2017 | Aiuti, Alessandro; Roncarolo, MARIA GRAZIA; Naldini, Luigi | |
| Genetic engineering of hematopoiesis: current stage of clinical translation and future perspectives | 1-gen-2019 | Naldini, Luigi | |
| HIF factors cooperate with PML-RARα to promote acute promyelocytic leukemia progression and relapse | 1-gen-2014 | Coltella, N; Percio, S; Valsecchi, R; Cuttano, R; Guarnerio, J; Ponzoni, Maurilio; Pandolfi, Pp; Melillo, G; Pattini, L; Bernardi, R. | |
| IFN gene/cell therapy curbs colorectal cancer colonization of the liver by acting on the hepatic microenvironment | 1-gen-2016 | Catarinella, Mario; Monestiroli, Andrea; Escobar, Giulia; Fiocchi, Amleto; Tran, Ngoc Lan; Aiolfi, Roberto; Marra, Paolo; Esposito, Antonio; Cipriani, Federica; Aldrighetti, Luca; Iannacone, Matteo; Naldini, Luigi; Guidotti, Luca G.; Sitia, Giovanni | |
| Integration profile of retroviral vector in gene therapy treated patients is cell-specific according to gene expression and chromatin conformation of target cell | 1-gen-2011 | Biasco, L; Ambrosi, Alessandro; Pellin, D; Bartholomae, C; Brigida, I; Roncarolo, MARIA GRAZIA; DI SERIO, Mariaclelia; von Kalle, C; Schmidt, M; Aiuti, Alessandro | |
| Intra-arterial transplantation of HLA-matched donor mesoangioblasts in Duchenne muscular dystrophy | 1-gen-2015 | Cossu, G; Previtali, Sc; Napolitano, S; Cicalese, Mp; Tedesco, Fs; Nicastro, F; Noviello, M; Roostalu, U; Natali Sora, Mg; Scarlato, M; De Pellegrin, M; Godi, C; Giuliani, S; Ciotti, F; Tonlorenzi, R; Lorenzetti, I; Rivellini, C; Benedetti, S; Gatti, R; Marktel, S; Mazzi, B; Tettamanti, A; Ragazzi, M; Imro, Ma; Marano, G; Ambrosi, Alessandro; Fiori, R; Sormani, Mp; Bonini, MARIA CHIARA; Venturini, M; Politi, Ls; Torrente, Y; Ciceri, Fabio | |
| Lentiviral vectors escape innate sensing but trigger p53 in human hematopoietic stem and progenitor cells | 1-gen-2017 | Piras, Francesco; Riba, Michela; Petrillo, Carolina; Lazarevic, Dejan; Cuccovillo, Ivan; Bartolaccini, Sara; Stupka, Elia; Gentner, Bernhard; Cittaro, Davide; Naldini, Luigi; Kajaste rudnitski, Anna | |
| Liver gene therapy by lentiviral vectors reverses anti-factor IX pre-existing immunity in haemophilic mice | 1-gen-2013 | Annoni, A; Cantore, A; Della Valle, P; Goudy, K; Akbarpour, M; Russo, F; Bartolaccini, S; D'Angelo, A; Roncarolo, MARIA GRAZIA; Naldini, Luigi | |
| Maternally inherited genetic variants of CADPS2 are present in Autism Spectrum Disorders and Intellectual Disability patients | 1-gen-2014 | Bonora, E; Graziano, C; Minopoli, F; Bacchelli, E; Magini, P; Diquigiovanni, C; Lomartire, S; Bianco, F; Vargiolu, M; Parchi, P; Marasco, E; Mantovani, V; Rampoldi, L; Trudu, M; Parmeggiani, A; Battaglia, A; Mazzone, L; Tortora, G; Maestrini, E; Seri, M; Romeo, G | |
| Modeling, optimization, and comparable efficacy of T cell and hematopoietic stem cell gene editing for treating hyper-IgM syndrome | 1-gen-2021 | Vavassori, V.; Mercuri, E.; Marcovecchio, G. E.; Castiello, M. C.; Schiroli, G.; Albano, L.; Margulies, C.; Buquicchio, F.; Fontana, E.; Beretta, S.; Merelli, I.; Cappelleri, A.; Rancoita, P. M. V.; Lougaris, V.; Plebani, A.; Kanariou, M.; Lankester, A.; Ferrua, F.; Scanziani, E.; Cotta-Ramusino, C.; Villa, A.; Naldini, L.; Genovese, P. | |
| Pathogen-specific B-cell receptors drive chronic lymphocytic leukemia by light-chain-dependent cross-reaction with autoantigens | 1-gen-2017 | Jiménez de Oya, Nereida; De Giovanni, Marco; Fioravanti, Jessica; Übelhart, Rudolf; Di Lucia, Pietro; Fiocchi, Amleto; Iacovelli, Stefano; Efremov, Dimitar G; Caligaris-Cappio, Federico; Jumaa, Hassan; Ghia, Paolo; Guidotti, Luca G; Iannacone, Matteo | |
| Pervasive supply of therapeutic lysosomal enzymes in the CNS of normal and Krabbe-affected non-human primates by intracerebral lentiviral gene therapy | 1-gen-2016 | Meneghini, Vasco; Lattanzi, Annalisa; Tiradani, Luigi; Bravo, Gabriele; Morena, Francesco; Sanvito, Francesca; Calabria, Andrea; Bringas, John; Fisher-Perkins, Jeanne M; Dufour, Jason P; Baker, Kate C; Doglioni, Claudio; Montini, Eugenio; Bunnell, Bruce A; Bankiewicz, Krystof; Martino, Sabata; Naldini, Luigi; Gritti, Angela | |
| Pharmacological or genetic inhibition of iNOS prevents cachexia-mediated muscle wasting and its associated metabolism defects | 1-gen-2021 | Sadek, J.; Hall, D. T.; Colalillo, B.; Omer, A.; Tremblay, A. -M. K.; Sanguin-Gendreau, V.; Muller, W.; Di Marco, S.; Bianchi, M. E.; Gallouzi, I. -E. | |
| Reversible immortalisation enables genetic correction of human muscle progenitors and engineering of next-generation human artificial chromosomes for Duchenne muscular dystrophy | 1-gen-2018 | Benedetti, Sara; Uno, Narumi; Hoshiya, Hidetoshi; Ragazzi, Martina; Ferrari, Giuliana; Kazuki, Yasuhiro; Moyle, Louise Anne; Tonlorenzi, Rossana; Lombardo, Angelo; Chaouch, Soraya; Mouly, Vincent; Moore, Marc; Popplewell, Linda; Kazuki, Kanako; Katoh, Motonobu; Naldini, Luigi; Dickson, George; Messina, Graziella; Oshimura, Mitsuo; Cossu, Giulio; Tedesco, Francesco Saverio | |
| Targeted gene therapy and cell reprogramming in Fanconi anemia | 1-gen-2014 | Rio, P; Baños, R; Lombardo, ANGELO LEONE; Quintana Bustamante, O; Alvarez, L; Garate, Z; Genovese, P; Almarza, E; Valeri, A; Díez, B; Navarro, S; Torres, Y; Trujillo, Jp; Murillas, R; Segovia, Jc; Samper, E; Surralles, J; Gregory, Pd; Holmes, Mc; Naldini, Luigi; Bueren, Ja |
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