MENEGHINI, VASCO

MENEGHINI, VASCO  

Facoltà di Medicina e Chirurgia  

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Risultati 1 - 20 di 23 (tempo di esecuzione: 0.041 secondi).
Titolo Data di pubblicazione Autore(i) File
A novel role for the Receptor for Advanced Glycation End-products in neural progenitor cells derived from adult SubVentricular Zone 1-gen-2010 Meneghini, Vasco; Francese, Maria Teresa; Carraro, Lorenzo; Grilli, Mariagrazia
An Optimized Lentiviral Vector Efficiently Corrects the Human Sickle Cell Disease Phenotype 1-gen-2018 Weber, Leslie; Poletti, Valentina; Magrin, Elisa; Antoniani, Chiara; Martin, Samia; Bayard, Charles; Sadek, Hanem; Felix, Tristan; Meneghini, Vasco; Antoniou, Michael N; El-Nemer, Wassim; Mavilio, Fulvio; Cavazzana, Marina; Andre-Schmutz, Isabelle; Miccio, Annarita
Combination of lentiviral and genome editing technologies for the treatment of sickle cell disease 1-gen-2022 Ramadier, Sophie; Chalumeau, Anne; Felix, Tristan; Othman, Nadia; Aknoun, Sherazade; Casini, Antonio; Maule, Giulia; Masson, Cecile; De Cian, Anne; Frati, Giacomo; Brusson, Megane; Concordet, Jean-Paul; Cavazzana, Marina; Cereseto, Anna; El Nemer, Wassim; Amendola, Mario; Wattellier, Benoit; Meneghini, Vasco; Miccio, Annarita
Delivery Platforms for CRISPR/Cas9 Genome Editing of Glial Cells in the Central Nervous System 1-gen-2021 Meneghini, Vasco; Peviani, Marco; Luciani, Marco; Zambonini, Giada; Gritti, Angela
Editing a γ-globin repressor binding site restores fetal hemoglobin synthesis and corrects the sickle cell disease phenotype 1-gen-2020 Weber, Leslie; Frati, Giacomo; Felix, Tristan; Hardouin, Giulia; Casini, Antonio; Wollenschlaeger, Clara; Meneghini, Vasco; Masson, Cecile; De Cian, Anne; Chalumeau, Anne; Mavilio, Fulvio; Amendola, Mario; Andre-Schmutz, Isabelle; Cereseto, Anna; El Nemer, Wassim; Concordet, Jean-Paul; Giovannangeli, Carine; Cavazzana, Marina; Miccio, Annarita
Editorial: Ex-vivo and in-vivo genome engineering for metabolic and neurometabolic diseases 1-gen-2023 Colella, P.; Meneghini, V.; Baldo, G.; Gomez-Ospina, N.
GATA Factor-Mediated Gene Regulation in Human Erythropoiesis 1-gen-2020 Romano, O.; Petiti, L.; Felix, T.; Meneghini, V.; Portafax, M.; Antoniani, C.; Amendola, M.; Bicciato, S.; Peano, C.; Miccio, A.
Generation of Human Induced Pluripotent Stem Cell-Derived Bona Fide Neural Stem Cells for Ex Vivo Gene Therapy of Metachromatic Leukodystrophy 1-gen-2017 Meneghini, Vasco; Frati, Giacomo; Sala, Davide; De Cicco, Silvia; Luciani, Marco; Cavazzin, Chiara; Paulis, Marianna; Mentzen, Wieslawa; Morena, Francesco; Giannelli, Serena; Sanvito, Francesca; Villa, Anna; Bulfone, Alessandro; Broccoli, Vania; Martino, Sabata; Gritti, Angela
High-mobility group box-1 protein and β-amyloid oligomers promote neuronal differentiation of adult hippocampal neural progenitors via receptor for advanced glycation end products/nuclear factor-κB axis: relevance for Alzheimer's disease 1-gen-2013 Meneghini, Vasco; Bortolotto, Valeria; Francese, Maria Teresa; Dellarole, Anna; Carraro, Lorenzo; Terzieva, Slavica; Grilli, Mariagrazia
Human iPSC-Based Models for the Development of Therapeutics Targeting Neurodegenerative Lysosomal Storage Diseases 1-gen-2020 Luciani, Marco; Gritti, Angela; Meneghini, Vasco
Human iPSC-based models highlight defective glial and neuronal differentiation from neural progenitor cells in metachromatic leukodystrophy 1-gen-2018 Frati, Giacomo; Luciani, Marco; Meneghini, Vasco; De Cicco, Silvia; Ståhlman, Marcus; Blomqvist, Maria; Grossi, Serena; Filocamo, Mirella; Morena, Francesco; Menegon, Andrea; Martino, Sabata; Gritti, Angela
In vivo Gene Therapy to the Liver and Nervous System: Promises and Challenges 1-gen-2022 Cantore, Alessio; Fraldi, Alessandro; Meneghini, Vasco; Gritti, Angela
Induction of fetal hemoglobin synthesis by CRISPR/Cas9-mediated editing of the human β-globin locus 1-gen-2018 Antoniani, Chiara; Meneghini, Vasco; Lattanzi, Annalisa; Felix, Tristan; Romano, Oriana; Magrin, Elisa; Weber, Leslie; Pavani, Giulia; El Hoss, Sara; Kurita, Ryo; Nakamura, Yukio; Cradick, Thomas J; Lundberg, Ante S; Porteus, Matthew; Amendola, Mario; El Nemer, Wassim; Cavazzana, Marina; Mavilio, Fulvio; Miccio, Annarita
Intracerebroventricular transplantation of human iPSC-derived neural stem cells (hiPSC-NSCs) into neonatal mice 1-gen-2022 Luciani, Marco; Garsia, Chiara; Mangiameli, Elisabeth; Meneghini, Vasco; Gritti, Angela
NF-κB Proteins in Adult Neurogenesis: Relevance for Learning and Memory in Physiology and Pathology 1-gen-2012 Grilli, Mariagrazia; Meneghini, Vasco
Novel TBX3 mutation data in families with Ulnar-Mammary syndrome indicate a genotype-phenotype relationship: mutations that do not disrupt the T-domain are associated with less severe limb defects 1-gen-2006 Meneghini, V; Sylvie, Odent; Natalia, Platonova; Aliana, Egeo; Giorgio, R MERLO
Optimization of CRISPR/Cas9 Delivery to Human Hematopoietic Stem and Progenitor Cells for Therapeutic Genomic Rearrangements 1-gen-2018 Lattanzi, A.; Meneghini, V.; Pavani, G.; Amor, F.; Ramadier, S.; Felix, T.; Antoniani, C.; Masson, C.; Alibeu, O.; Lee, C.; Porteus, M. H.; Bao, G.; Amendola, M.; Mavilio, F.; Miccio, A.
Pervasive supply of therapeutic lysosomal enzymes in the CNS of normal and Krabbe-affected non-human primates by intracerebral lentiviral gene therapy 1-gen-2016 Meneghini, Vasco; Lattanzi, Annalisa; Tiradani, Luigi; Bravo, Gabriele; Morena, Francesco; Sanvito, Francesca; Calabria, Andrea; Bringas, John; Fisher-Perkins, Jeanne M; Dufour, Jason P; Baker, Kate C; Doglioni, Claudio; Montini, Eugenio; Bunnell, Bruce A; Bankiewicz, Krystof; Martino, Sabata; Naldini, Luigi; Gritti, Angela
RECOMBINANT LENTIVIRAL VECTOR FOR STEM CELL-BASED GENE THERAPY OF SICKLE CELL DISORDER 1-gen-2018 Miccio, Annarita; Meneghini, Vasco
TBX3, the gene mutated in ulnar-mammary syndrome, promotes growth of mammary epithelial cells via repression of p19ARF, independently of p53 1-gen-2007 Natalia, Platonova; Maddalena, Scotti; Polina, Babich; Gloria, Bertoli; Elena, Mento; Meneghini, V; Aliana, Egeo; Ileana, Zucchi; Giorgio, Merlo