NALDINI, LUIGI

NALDINI, LUIGI  

Facoltà di Medicina e Chirurgia  

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Titolo Data di pubblicazione Autore(i) File
'Advanced' generation lentivirruses as efficient vectors for cardiomyocyte gene transduction in vitro and in vivo 1-gen-2003 Bonci, D; Cittadini, A; Latronico, Mvg; Borello, U; Aycock, Jk; Drusco, A; Innocenzi, A; Follenzi, A; Lavitrano, M; Monti, Mg; Rossjr, J; Naldini, Luigi; Peschle, C; Cossu, G; Condorelli, G.
A case of T-cell acute lymphoblastic leukemia in retroviral gene therapy for ADA-SCID 1-gen-2024 Cesana, D.; Cicalese, M. P.; Calabria, A.; Merli, P.; Caruso, R.; Volpin, M.; Rudilosso, L.; Migliavacca, M.; Barzaghi, F.; Fossati, C.; Gazzo, F.; Pizzi, S.; Ciolfi, A.; Bruselles, A.; Tucci, F.; Spinozzi, G.; Pais, G.; Benedicenti, F.; Barcella, M.; Merelli, I.; Gallina, P.; Giannelli, S.; Dionisio, F.; Scala, S.; Casiraghi, M.; Strocchio, L.; Vinti, L.; Pacillo, L.; Draghi, E.; Cesana, M.; Riccardo, S.; Colantuono, C.; Six, E.; Cavazzana, M.; Carlucci, F.; Schmidt, M.; Cancrini, C.; Ciceri, F.; Vago, L.; Cacchiarelli, D.; Gentner, B.; Naldini, L.; Tartaglia, M.; Montini, E.; Locatelli, F.; Aiuti, A.
A Comeback for Gene Therapy 1-gen-2009 Naldini, Luigi
A distinguishing gene signature shared by tumor-infiltrating Tie2-expressing monocytes (TEMs), blood “resident” monocytes and embryonic macrophages suggests common functions and developmental relationships 1-gen-2009 Pucci, Venneri; Biziato, Nonis; Moi, Sica; DI SERIO, Mariaclelia; Naldini, Luigi; De, Palma
A double-switch vector system positively regulates transgene expression by endogenous microRNA expression (miR-ON vector) 1-gen-2013 Amendola, M; Giustacchini, A; Gentner, B; Naldini, Luigi
A foundation for universal T-cell based immunotherapy: T cells engineered to express a CD19-specific chimeric-antigen-receptor and eliminate expression of endogenous TCR 1-gen-2012 Torikai, H1; Reik, A; Liu, Pq; Zhou, Y; Zhang, L; Maiti, S; Huls, H; Miller, Jc; Kebriaei, P; Rabinovitch, B; Lee, Da; Champlin, Re; Bonini, MARIA CHIARA; Naldini, Luigi; Rebar, Ej; Gregory, Pd; Holmes, Mc; Cooper, Lj
A FUNCTIONAL DOMAIN IN THE HEAVY-CHAIN OF SCATTER FACTOR HEPATOCYTE GROWTH-FACTOR BINDS THE C-MET RECEPTOR AND INDUCES CELL-DISSOCIATION BUT NOT MITOGENESIS 1-gen-1992 Hartmann, G; Naldini, Luigi; Weidner, Km; Sachs, M; Vigna, E; Comoglio, Pm; Birchmeier, W.
A gene mutatioons reinforces genotype-phenotype correlation in metachromatic leukodystrophy 1-gen-2009 Cesani, M; Capotondo, A; Plati, T; Sergi, Ls; Fumagalli, F; Roncarolo, Mg; Naldini, L; Comi, Giancarlo; Sessa, M; Biffi, A.
A human immunodeficiency virus type 1 pol gene-derived sequence (cPPT/CTS) increases the efficiency of transduction of human nondividing monocytes and T lymphocytes by lentiviral vectors 1-gen-2002 Manganini, M; Serafini, M; Bambacioni, F; Casati, C; Erba, E; Follenzi, A; Naldini, Luigi; Bernasconi, S; Gaipa, G; Rambaldi, A; Biondi, A; Golay, J; Introna, M.
A Mechanistic Role For Mir-126, a Hematopoietic Stem Cell Microrna, In Acute Leukemias 1-gen-2013 Giustacchini, A; Nucera, S; Lechman, Er; Fanciullo, C; Boccalatte, Fe; Plati, T; Ranghetti, A; Vago, L; Bernardi, M; Ponzoni, M; Dick, Je; Naldini, L; Gentner, B
A MicroRNA-regulated and GP64-pseudotyped Lentiviral Vector Mediates Stable Expression of FVIII in a Murine Model of Hemophilia A 1-gen-2011 Matsui, H; Hegadorn, C; Ozelo, M; Burnett, E; Tuttle, A; Labelle, A; Mccray, Pb; Naldini, Luigi; Brown, B; Hough, C; Lillicrap, D.
A microRNA-regulated lentiviral vector mediates stable correction of hemophilia B mice 1-gen-2007 Brown, Bd; Cantore, A; Annoni, A; Sergi, Ls; Lombardo, ANGELO LEONE; Della Valle, P; D'Angelo, A; Naldini, Luigi
A miRNA-Based System for Selecting and Maintaining the Pluripotent State in Human Induced Pluripotent Stem Cells 1-gen-2011 Di Stefano, B.; Maffioletti, S. M.; Gentner, B.; Ungaro, F.; Schira, G.; Broccoli, V.; Naldini, Luigi
A New-Generation Stable Inducible Packaging Cell Line for Lentiviral Vectors 1-gen-2001 Farson, D; Witt, R; Mcguinness, R; Dull, T; Kelly, M; Song, J; Radeke, R; Bukovsky, A; Consiglio, A; Naldini, Luigi
A role for miR-155 in enabling tumor-infiltrating innate immune cells to mount effective antitumor responses in mice 1-gen-2013 Zonari, E; Pucci, F; Saini, M; Mazzieri, R; Politi, Ls; Gentner, B; Naldini, Luigi
Activation of the protein-tyrosine kinase associated with the bombesin receptor complex in small cell lung carcinomas. 1-gen-1988 Gaudino, G; Cirillo, D; Naldini, Luigi; Rossino, P; Comoglio, P. M.
Adopt a moratorium on heritable genome editing 1-gen-2019 Lander, E. S; Baylis, F; Zhang, F; Charpentier, E; Berg, P; on behalf of specialists from seven countries call for an international governance, Framework; Naldini, L
Advanced cell-based therapies for the treatment of primary immunodeficiency (Cell-PID) 1-gen-2014 Aiuti, A.; Roncarolo, M. G.; Cavazzana-Calvo, M.; Thrasher, A.; Grez, M.; Lapidot, T.; Waskow, C.; Wagemaker, G.; Rossi, P.; Baum, C.; Bovolenta, C.; Johnston, I.; Hollaender, G. -A.; Mueller, B.; Koubi, D.; Kuhlcke, K.; Cetinkaya, D.; Reichenbach, J.; Gaspar, B.; Naldini, L.
An innovative platform approach for the development of ex-vivo gene therapies for the treatment of lysosomal storage diseases with skeletal involvement 1-gen-2022 Forni, C; Gabaldo, M; Crippa, S; Scala, S; Consiglieri, G; Tucci, F; Passerini, L; Gritti, A; Gregori, S; Ferrari, G; Albertini, P; Galimberti, Mg; Valsecchi, A; Corti, A; Zancan, S Scarpa M; Parini, R; Naldini, L; Gentner, B; Bernardo, Me; Aiuti, A
An unbiased genome-wide analysis of zinc-finger nuclease specificity 1-gen-2011 Gabriel, R; Lombardo, ANGELO LEONE; Arens, A; Miller, Jc; Genovese, P; Kaeppel, C; Nowrouzi, A; Bartholomae, Cc; Wang, J; Friedman, G; Holmes, Mc; Gregory, Pd; Glimm, H; Schmidt, M; Naldini, Luigi; von Kalle, C.