Early sulfatide storage and progressive neuronal and glial cell dysfunction revealed by human iPSC-based models of metachromatic leukodystrophy are rescued by lentiviral-mediated restoration of ARSA activity / Frati, ; G, ; Luciani, ; M, ; Meneghini, ; V, ; De, Cicco; S, ; Stahlman, ; M, ; Grossi, ; S, ; Morena, ; F, ; Blomqvist, ; M, ; Filocamo, ; M, ; Martino, ; S, ; Gritti, A. - In: HUMAN GENE THERAPY. - ISSN 1043-0342. - (2017).

Early sulfatide storage and progressive neuronal and glial cell dysfunction revealed by human iPSC-based models of metachromatic leukodystrophy are rescued by lentiviral-mediated restoration of ARSA activity

Gritti A
2017-01-01

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Utilizza questo identificativo per citare o creare un link a questo documento: https://hdl.handle.net/20.500.11768/160272
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