Early sulfatide storage and progressive neuronal and glial cell dysfunction revealed by human iPSC-based models of metachromatic leukodystrophy are rescued by lentiviral-mediated restoration of ARSA activity / Frati, ., G, ., Luciani, ., M, ., Meneghini, ., V, ., De, C., S, ., Stahlman, ., M, ., Grossi, ., S, ., Morena, ., F, ., Blomqvist, ., M, ., Filocamo, ., M, ., Martino, ., S, ., et al.. - In: HUMAN GENE THERAPY. - ISSN 1043-0342. - (2017).

Early sulfatide storage and progressive neuronal and glial cell dysfunction revealed by human iPSC-based models of metachromatic leukodystrophy are rescued by lentiviral-mediated restoration of ARSA activity

Gritti A
2017-01-01

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Utilizza questo identificativo per citare o creare un link a questo documento: https://hdl.handle.net/20.500.11768/160272
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