Wolfram syndrome: investigating the visual phenotype of Wolfram mice models, the functionality of wolframin protein, and the role of astrocytes in the pathology; developing a AAV vector-based gene therapy to treat the optic atrophy in Wolfram mice models

Wolfram syndrome: investigating the visual phenotype of Wolfram mice models, the functionality of wolframin protein, and the role of astrocytes in the pathology; developing a AAV vector-based gene therapy to treat the optic atrophy in Wolfram mice models

Unveiling the pathophysiological basis and developing a gene therapy approach for Wolfram syndrome / Niccolò Natanaele Vanni , 2026 Mar 13. 38. ciclo, Anno Accademico 2024/2025.

Unveiling the pathophysiological basis and developing a gene therapy approach for Wolfram syndrome

VANNI, NICCOLÒ NATANAELE
2026-03-13

Abstract

Wolfram syndrome: investigating the visual phenotype of Wolfram mice models, the functionality of wolframin protein, and the role of astrocytes in the pathology; developing a AAV vector-based gene therapy to treat the optic atrophy in Wolfram mice models
13-mar-2026
BIO/13 - BIOLOGIA APPLICATA
Unveiling the pathophysiological basis and developing a gene therapy approach for Wolfram syndrome / Niccolò Natanaele Vanni , 2026 Mar 13. 38. ciclo, Anno Accademico 2024/2025.
Doctoral Thesis
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Utilizza questo identificativo per citare o creare un link a questo documento: https://hdl.handle.net/20.500.11768/197336
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