Sfoglia per Rivista
Coexpression of CD49b and LAG-3 identifies human and mouse T regulatory type 1 cells
2013-01-01 Gagliani, N; Magnani, Cf; Huber, S; Gianolini, Me; Pala, M; Licona Limon, P; Guo, B; Herbert, Dr; Bulfone, A; Trentini, F; DI SERIO, Mariaclelia; Bacchetta, R; Andreani, M; Brockmann, L; Gregori, S; Flavell, Ra; Roncarolo, MARIA GRAZIA
Common noncoding UMOD promoter variants induce salt-sensitive hypertension and kidney damage by increasing uromodulin expression
2013-01-01 Trudu, M; Janas, S; Lanzani, C; Debaix, H; Schaeffer, C; Ikehata, M; Citterio, L; Demaretz, S; Trevisani, F; Ristagno, G; Glaudemans, B; Laghmanik, ; Dell’Antonio, G; the Swiss Kidney Project on Genes in Hypertension team, 11; Loffing, J; Rastaldi, Mg; Manunta, Paolo; Devuyst, O; Rampolli, L.; Rampoldi, Luca
Comprehensive genomic access to vector integration in clinical gene therapy
2009-01-01 Gabriel, R; Eckenberg, R; Paruzynski, A; Bartholomae, Cc; Nowrouzi, A; Arens, A; Howe, Sj; Recchia, A; Cattoglio, C; Wang, W; Faber, K; Schwarzwaelder, K; Kirsten, R; Deichmann, A; Ball, Cr; Balaggan, Ks; Yáñez Muñoz, Rj; Ali, Rr; Gaspar, Hb; Biasco, L; Aiuti, Alessandro; Cesana, D; Montini, E; Naldini, Luigi; Cohen Haguenauer, O; Mavilio, F; Thrasher, Aj; Glimm, H; von Kalle, C; Saurin, W; Schmidt, M.
Correction of junctional epidermolysis bullosa by transplantation of genetically modified epidermal stem cells
2006-01-01 Mavilio, F; Pellegrini, G; Ferrari, S; Di Nunzio, F; Di Iorio, E; Recchia, A; Maruggi, G; Ferrari, Giuliana; Provasi, E; Bonini, MARIA CHIARA; Capurro, S; Conti, A; Magnoni, C; Giannetti, A; De Luca, M.
Dynamics of genetically engineered hematopoietic stem and progenitor cells after autologous transplantation in humans
2018-01-01 Scala, S.; Basso-Ricci, L.; Dionisio, F.; Pellin, D.; Giannelli, S.; Salerio, F. A.; Leonardelli, L.; Cicalese, M. P.; Ferrua, F.; Aiuti, A.; Biasco, L.
Early treatment of COVID-19 with anakinra guided by soluble urokinase plasminogen receptor plasma levels: a double-blind, randomized controlled phase 3 trial
2021-01-01 Kyriazopoulou, E.; Poulakou, G.; Milionis, H.; Metallidis, S.; Adamis, G.; Tsiakos, K.; Fragkou, A.; Rapti, A.; Damoulari, C.; Fantoni, M.; Kalomenidis, I.; Chrysos, G.; Angheben, A.; Kainis, I.; Alexiou, Z.; Castelli, F.; Serino, F. S.; Tsilika, M.; Bakakos, P.; Nicastri, E.; Tzavara, V.; Kostis, E.; Dagna, L.; Koufargyris, P.; Dimakou, K.; Savvanis, S.; Tzatzagou, G.; Chini, M.; Cavalli, Giulio.; Bassetti, M.; Katrini, K.; Kotsis, V.; Tsoukalas, G.; Selmi, C.; Bliziotis, I.; Samarkos, M.; Doumas, M.; Ktena, S.; Masgala, A.; Papanikolaou, I.; Kosmidou, M.; Myrodia, D. -M.; Argyraki, A.; Cardellino, C. S.; Koliakou, K.; Katsigianni, E. -I.; Rapti, V.; Giannitsioti, E.; Cingolani, A.; Micha, S.; Akinosoglou, K.; Liatsis-Douvitsas, O.; Symbardi, S.; Gatselis, N.; Mouktaroudi, M.; Ippolito, G.; Florou, E.; Kotsaki, A.; Netea, M. G.; Eugen-Olsen, J.; Kyprianou, M.; Panagopoulos, P.; Dalekos, G. N.; Giamarellos-Bourboulis, E. J.
Editing T cell specificity towards leukemia by zinc finger nucleases and lentiviral gene transfer
2012-01-01 Provasi, E; Genovese, P; Lombardo, ANGELO LEONE; Magnani, Z; Liu Pei, Q; Reik, A; Chu, V; Paschon, D. E.; Zhang, L; Kuball, J; Camisa, B; Bondanza, Attilio; Casorati, G; Ponzoni, Maurilio; Ciceri, Fabio; Bordignon, Claudio; Greenberg, P. D.; Holmes, Mc; Gregory, Pd; Naldini, Luigi; Bonini, MARIA CHIARA
Endogenous microRNA Regulation Suppresses Transgene Expression in Hematopoietic Lineages and Enables Stable Gene Transfer
2006-01-01 D, Brown B.; Venneri M., A.; Zingale, A; Nulll, nullSergi Sergi; Naldini, Luigi
Ensuring a future for gene therapy for rare diseases
2022-01-01 Aiuti, A.; Pasinelli, F.; Naldini, L.
Epithelial calcineurin controls microbiota-dependent intestinal tumor development
2016-01-01 Peuker, K; Muff, S; Wang, J; Künzel, S; Bosse, E; Zeissig, Y; Luzzi, G; Basic, M; Strigli, A; Ulbricht, A; Kaser, A; Arlt, A; Chavakis, T; van den Brink, Gr; Schafmayer, C; Egberts, J. H.; Becker, T; Bianchi, MARCO EMILIO; Bleich, A; Röcken, C; Hampe, J; Schreiber, S; Baines, Jf; Blumberg, Rs; Zeissig, S.
Generation of primary antigen-specific human T- and B-cell responses in immunocompetent SCID-hu mice
2000-01-01 Carballido, J. M.; Namikawa, R.; CARBALLIDO PERIG, N.; Antonenko, S.; Roncarolo, MARIA GRAZIA; DE VRIES, J. E.
Genome editing: a tool for research and therapy: Targeted genome editing hits the clinic
2014-01-01 Lombardo, ANGELO LEONE; Naldini, Luigi
Has SARS-CoV-2 reached peak fitness?
2021-01-01 Burioni, R.; Topol, E. J.
Human and mouse single-nucleus transcriptomics reveal TREM2-dependent and TREM2-independent cellular responses in Alzheimer’s disease
2020-01-01 Zhou, Y.; Song, W. M.; Andhey, P. S.; Swain, A.; Levy, T.; Miller, K. R.; Poliani, P. L.; Cominelli, M.; Grover, S.; Gilfillan, S.; Cella, M.; Ulland, T. K.; Zaitsev, K.; Miyashita, A.; Ikeuchi, T.; Sainouchi, M.; Kakita, A.; Bennett, D. A.; Schneider, J. A.; Nichols, M. R.; Beausoleil, S. A.; Ulrich, J. D.; Holtzman, D. M.; Artyomov, M. N.; Colonna, M.
Immune reconstitution in ADA-SCID after PBL gene therapy and discontinuation of enzyme replacement
2002-01-01 Aiuti, Alessandro; Vai, S; Mortellaro, A; Casorati, G; Ficara, F; Andolfi, G; Ferrari, Giuliana; Tabucchi, A; Carlucci, F; Ochs, Hd; Notarangelo, Ld; Roncarolo, MARIA GRAZIA; Bordignon, Claudio
Immune signature drives leukemia escape and relapse after hematopoietic cell transplantation
2019-01-01 Toffalori, C.; Zito, L.; Gambacorta, V.; Riba, M.; Oliveira, G.; Bucci, G.; Barcella, M.; Spinelli, O.; Greco, R.; Crucitti, L.; Cieri, N.; Noviello, M.; Manfredi, F.; Montaldo, E.; Ostuni, R.; Naldini, M. M.; Gentner, B.; Waterhouse, M.; Zeiser, R.; Finke, J.; Hanoun, M.; Beelen, D. W.; Gojo, I.; Luznik, L.; Onozawa, M.; Teshima, T.; Devillier, R.; Blaise, D.; Halkes, C. J. M.; Griffioen, M.; Carrabba, M. G.; Bernardi, M.; Peccatori, J.; Barlassina, C.; Stupka, E.; Lazarevic, D.; Tonon, G.; Rambaldi, A.; Cittaro, D.; Bonini, C.; Fleischhauer, K.; Ciceri, F.; Vago, L.
In vivo gene therapy of metachromatic leukodystrophy by lentiviral vectors: correction of neuropathology and protection against learning impairments in affected mice
2001-01-01 Consiglio, A.; Quattrini, A; Martino, S.; Bensadoun, J. C.; Dolcetta, D.; Trojani, A.; Benaglia, G.; Marchesini, S.; Cestari, V.; Oliviero, A; Bordignon, Claudio; Naldini, Luigi
Induction of a non-encephalitogenic T2 helper-cell autoimmune response in multiple sclerosis after administration of an altered peptide ligand in a placebo-controlled, randomized phase II trial.
2000-01-01 Kappos, L; Comi, G; Panitch, H; Oger, J; Antel, J; Conlon, P; Steinman, L; the APL in Relapsing MS Study Group, With; Filippi, Massimo
Inserting optimism into gene therapy
2006-01-01 Naldini, Luigi
Intrabone hematopoietic stem cell gene therapy for adult and pediatric patients affected by transfusion-dependent ß-thalassemia
2019-01-01 Marktel, Sarah; Scaramuzza, Samantha; Cicalese, Maria Pia; Giglio, Fabio; Galimberti, Stefania; Lidonnici, Maria Rosa; Calbi, Valeria; Assanelli, Andrea; Bernardo, Maria Ester; Rossi, Claudia; Calabria, Andrea; Milani, Raffaella; Gattillo, Salvatore; Benedicenti, Fabrizio; Spinozzi, Giulio; Aprile, Annamaria; Bergami, Alessandra; Casiraghi, Miriam; Consiglieri, Giulia; Masera, Nicoletta; D’Angelo, Emanuela; Mirra, Nadia; Origa, Raffaella; Tartaglione, Immacolata; Perrotta, Silverio; Winter, Robert; Coppola, Milena; Viarengo, Gianluca; Santoleri, Luca; Graziadei, Giovanna; Gabaldo, Michela; Valsecchi, Maria Grazia; Montini, Eugenio; Naldini, Luigi; Cappellini, Maria Domenica; Ciceri, Fabio; Aiuti, Alessandro; Ferrari, Giuliana
Titolo | Data di pubblicazione | Autore(i) | File |
---|---|---|---|
Coexpression of CD49b and LAG-3 identifies human and mouse T regulatory type 1 cells | 1-gen-2013 | Gagliani, N; Magnani, Cf; Huber, S; Gianolini, Me; Pala, M; Licona Limon, P; Guo, B; Herbert, Dr; Bulfone, A; Trentini, F; DI SERIO, Mariaclelia; Bacchetta, R; Andreani, M; Brockmann, L; Gregori, S; Flavell, Ra; Roncarolo, MARIA GRAZIA | |
Common noncoding UMOD promoter variants induce salt-sensitive hypertension and kidney damage by increasing uromodulin expression | 1-gen-2013 | Trudu, M; Janas, S; Lanzani, C; Debaix, H; Schaeffer, C; Ikehata, M; Citterio, L; Demaretz, S; Trevisani, F; Ristagno, G; Glaudemans, B; Laghmanik, ; Dell’Antonio, G; the Swiss Kidney Project on Genes in Hypertension team, 11; Loffing, J; Rastaldi, Mg; Manunta, Paolo; Devuyst, O; Rampolli, L.; Rampoldi, Luca | |
Comprehensive genomic access to vector integration in clinical gene therapy | 1-gen-2009 | Gabriel, R; Eckenberg, R; Paruzynski, A; Bartholomae, Cc; Nowrouzi, A; Arens, A; Howe, Sj; Recchia, A; Cattoglio, C; Wang, W; Faber, K; Schwarzwaelder, K; Kirsten, R; Deichmann, A; Ball, Cr; Balaggan, Ks; Yáñez Muñoz, Rj; Ali, Rr; Gaspar, Hb; Biasco, L; Aiuti, Alessandro; Cesana, D; Montini, E; Naldini, Luigi; Cohen Haguenauer, O; Mavilio, F; Thrasher, Aj; Glimm, H; von Kalle, C; Saurin, W; Schmidt, M. | |
Correction of junctional epidermolysis bullosa by transplantation of genetically modified epidermal stem cells | 1-gen-2006 | Mavilio, F; Pellegrini, G; Ferrari, S; Di Nunzio, F; Di Iorio, E; Recchia, A; Maruggi, G; Ferrari, Giuliana; Provasi, E; Bonini, MARIA CHIARA; Capurro, S; Conti, A; Magnoni, C; Giannetti, A; De Luca, M. | |
Dynamics of genetically engineered hematopoietic stem and progenitor cells after autologous transplantation in humans | 1-gen-2018 | Scala, S.; Basso-Ricci, L.; Dionisio, F.; Pellin, D.; Giannelli, S.; Salerio, F. A.; Leonardelli, L.; Cicalese, M. P.; Ferrua, F.; Aiuti, A.; Biasco, L. | |
Early treatment of COVID-19 with anakinra guided by soluble urokinase plasminogen receptor plasma levels: a double-blind, randomized controlled phase 3 trial | 1-gen-2021 | Kyriazopoulou, E.; Poulakou, G.; Milionis, H.; Metallidis, S.; Adamis, G.; Tsiakos, K.; Fragkou, A.; Rapti, A.; Damoulari, C.; Fantoni, M.; Kalomenidis, I.; Chrysos, G.; Angheben, A.; Kainis, I.; Alexiou, Z.; Castelli, F.; Serino, F. S.; Tsilika, M.; Bakakos, P.; Nicastri, E.; Tzavara, V.; Kostis, E.; Dagna, L.; Koufargyris, P.; Dimakou, K.; Savvanis, S.; Tzatzagou, G.; Chini, M.; Cavalli, Giulio.; Bassetti, M.; Katrini, K.; Kotsis, V.; Tsoukalas, G.; Selmi, C.; Bliziotis, I.; Samarkos, M.; Doumas, M.; Ktena, S.; Masgala, A.; Papanikolaou, I.; Kosmidou, M.; Myrodia, D. -M.; Argyraki, A.; Cardellino, C. S.; Koliakou, K.; Katsigianni, E. -I.; Rapti, V.; Giannitsioti, E.; Cingolani, A.; Micha, S.; Akinosoglou, K.; Liatsis-Douvitsas, O.; Symbardi, S.; Gatselis, N.; Mouktaroudi, M.; Ippolito, G.; Florou, E.; Kotsaki, A.; Netea, M. G.; Eugen-Olsen, J.; Kyprianou, M.; Panagopoulos, P.; Dalekos, G. N.; Giamarellos-Bourboulis, E. J. | |
Editing T cell specificity towards leukemia by zinc finger nucleases and lentiviral gene transfer | 1-gen-2012 | Provasi, E; Genovese, P; Lombardo, ANGELO LEONE; Magnani, Z; Liu Pei, Q; Reik, A; Chu, V; Paschon, D. E.; Zhang, L; Kuball, J; Camisa, B; Bondanza, Attilio; Casorati, G; Ponzoni, Maurilio; Ciceri, Fabio; Bordignon, Claudio; Greenberg, P. D.; Holmes, Mc; Gregory, Pd; Naldini, Luigi; Bonini, MARIA CHIARA | |
Endogenous microRNA Regulation Suppresses Transgene Expression in Hematopoietic Lineages and Enables Stable Gene Transfer | 1-gen-2006 | D, Brown B.; Venneri M., A.; Zingale, A; Nulll, nullSergi Sergi; Naldini, Luigi | |
Ensuring a future for gene therapy for rare diseases | 1-gen-2022 | Aiuti, A.; Pasinelli, F.; Naldini, L. | |
Epithelial calcineurin controls microbiota-dependent intestinal tumor development | 1-gen-2016 | Peuker, K; Muff, S; Wang, J; Künzel, S; Bosse, E; Zeissig, Y; Luzzi, G; Basic, M; Strigli, A; Ulbricht, A; Kaser, A; Arlt, A; Chavakis, T; van den Brink, Gr; Schafmayer, C; Egberts, J. H.; Becker, T; Bianchi, MARCO EMILIO; Bleich, A; Röcken, C; Hampe, J; Schreiber, S; Baines, Jf; Blumberg, Rs; Zeissig, S. | |
Generation of primary antigen-specific human T- and B-cell responses in immunocompetent SCID-hu mice | 1-gen-2000 | Carballido, J. M.; Namikawa, R.; CARBALLIDO PERIG, N.; Antonenko, S.; Roncarolo, MARIA GRAZIA; DE VRIES, J. E. | |
Genome editing: a tool for research and therapy: Targeted genome editing hits the clinic | 1-gen-2014 | Lombardo, ANGELO LEONE; Naldini, Luigi | |
Has SARS-CoV-2 reached peak fitness? | 1-gen-2021 | Burioni, R.; Topol, E. J. | |
Human and mouse single-nucleus transcriptomics reveal TREM2-dependent and TREM2-independent cellular responses in Alzheimer’s disease | 1-gen-2020 | Zhou, Y.; Song, W. M.; Andhey, P. S.; Swain, A.; Levy, T.; Miller, K. R.; Poliani, P. L.; Cominelli, M.; Grover, S.; Gilfillan, S.; Cella, M.; Ulland, T. K.; Zaitsev, K.; Miyashita, A.; Ikeuchi, T.; Sainouchi, M.; Kakita, A.; Bennett, D. A.; Schneider, J. A.; Nichols, M. R.; Beausoleil, S. A.; Ulrich, J. D.; Holtzman, D. M.; Artyomov, M. N.; Colonna, M. | |
Immune reconstitution in ADA-SCID after PBL gene therapy and discontinuation of enzyme replacement | 1-gen-2002 | Aiuti, Alessandro; Vai, S; Mortellaro, A; Casorati, G; Ficara, F; Andolfi, G; Ferrari, Giuliana; Tabucchi, A; Carlucci, F; Ochs, Hd; Notarangelo, Ld; Roncarolo, MARIA GRAZIA; Bordignon, Claudio | |
Immune signature drives leukemia escape and relapse after hematopoietic cell transplantation | 1-gen-2019 | Toffalori, C.; Zito, L.; Gambacorta, V.; Riba, M.; Oliveira, G.; Bucci, G.; Barcella, M.; Spinelli, O.; Greco, R.; Crucitti, L.; Cieri, N.; Noviello, M.; Manfredi, F.; Montaldo, E.; Ostuni, R.; Naldini, M. M.; Gentner, B.; Waterhouse, M.; Zeiser, R.; Finke, J.; Hanoun, M.; Beelen, D. W.; Gojo, I.; Luznik, L.; Onozawa, M.; Teshima, T.; Devillier, R.; Blaise, D.; Halkes, C. J. M.; Griffioen, M.; Carrabba, M. G.; Bernardi, M.; Peccatori, J.; Barlassina, C.; Stupka, E.; Lazarevic, D.; Tonon, G.; Rambaldi, A.; Cittaro, D.; Bonini, C.; Fleischhauer, K.; Ciceri, F.; Vago, L. | |
In vivo gene therapy of metachromatic leukodystrophy by lentiviral vectors: correction of neuropathology and protection against learning impairments in affected mice | 1-gen-2001 | Consiglio, A.; Quattrini, A; Martino, S.; Bensadoun, J. C.; Dolcetta, D.; Trojani, A.; Benaglia, G.; Marchesini, S.; Cestari, V.; Oliviero, A; Bordignon, Claudio; Naldini, Luigi | |
Induction of a non-encephalitogenic T2 helper-cell autoimmune response in multiple sclerosis after administration of an altered peptide ligand in a placebo-controlled, randomized phase II trial. | 1-gen-2000 | Kappos, L; Comi, G; Panitch, H; Oger, J; Antel, J; Conlon, P; Steinman, L; the APL in Relapsing MS Study Group, With; Filippi, Massimo | |
Inserting optimism into gene therapy | 1-gen-2006 | Naldini, Luigi | |
Intrabone hematopoietic stem cell gene therapy for adult and pediatric patients affected by transfusion-dependent ß-thalassemia | 1-gen-2019 | Marktel, Sarah; Scaramuzza, Samantha; Cicalese, Maria Pia; Giglio, Fabio; Galimberti, Stefania; Lidonnici, Maria Rosa; Calbi, Valeria; Assanelli, Andrea; Bernardo, Maria Ester; Rossi, Claudia; Calabria, Andrea; Milani, Raffaella; Gattillo, Salvatore; Benedicenti, Fabrizio; Spinozzi, Giulio; Aprile, Annamaria; Bergami, Alessandra; Casiraghi, Miriam; Consiglieri, Giulia; Masera, Nicoletta; D’Angelo, Emanuela; Mirra, Nadia; Origa, Raffaella; Tartaglione, Immacolata; Perrotta, Silverio; Winter, Robert; Coppola, Milena; Viarengo, Gianluca; Santoleri, Luca; Graziadei, Giovanna; Gabaldo, Michela; Valsecchi, Maria Grazia; Montini, Eugenio; Naldini, Luigi; Cappellini, Maria Domenica; Ciceri, Fabio; Aiuti, Alessandro; Ferrari, Giuliana |
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