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Mostrati risultati da 1 a 20 di 43
Titolo Data di pubblicazione Autore(i) File
A new chance for SCID gene therapy 1-gen-1998 Bordignon, Claudio
Access to gene therapy for rare diseases when commercialization is not fit for purpose 1-gen-2023 Fox, T.; Bueren, J.; Candotti, F.; Fischer, A.; Aiuti, A.; Lankester, A.; Albert, M.; Bernardo, M. E.; Cavazzana, M.; Ehl, S.; Neven, B.; Prevot, J.; Schambach, A.; Sevilla, J.; Thrasher, A.; Wynn, R.; Booth, C.
Assessing the human immune response to SARS-CoV-2 variants 1-gen-2021 Burioni, R.; Topol, E. J.
Author Correction: Early treatment of COVID-19 with anakinra guided by soluble urokinase plasminogen receptor plasma levels: a double-blind, randomized controlled phase 3 trial (Nature Medicine, (2021), 27, 10, (1752-1760), 10.1038/s41591-021-01499-z) 1-gen-2021 Kyriazopoulou, E.; Poulakou, G.; Milionis, H.; Metallidis, S.; Adamis, G.; Tsiakos, K.; Fragkou, A.; Rapti, A.; Damoulari, C.; Fantoni, M.; Kalomenidis, I.; Chrysos, G.; Angheben, A.; Kainis, I.; Alexiou, Z.; Castelli, F.; Serino, F. S.; Tsilika, M.; Bakakos, P.; Nicastri, E.; Tzavara, V.; Kostis, E.; Dagna, L.; Koufargyris, P.; Dimakou, K.; Savvanis, S.; Tzatzagou, G.; Chini, M.; Cavalli, G.; Bassetti, M.; Katrini, K.; Kotsis, V.; Tsoukalas, G.; Selmi, C.; Bliziotis, I.; Samarkos, M.; Doumas, M.; Ktena, S.; Masgala, A.; Papanikolaou, I.; Kosmidou, M.; Myrodia, D. -M.; Argyraki, A.; Cardellino, C. S.; Koliakou, K.; Katsigianni, E. -I.; Rapti, V.; Giannitsioti, E.; Cingolani, A.; Micha, S.; Akinosoglou, K.; Liatsis-Douvitsas, O.; Symbardi, S.; Gatselis, N.; Mouktaroudi, M.; Ippolito, G.; Florou, E.; Kotsaki, A.; Netea, M. G.; Eugen-Olsen, J.; Kyprianou, M.; Panagopoulos, P.; Dalekos, G. N.; Giamarellos-Bourboulis, E. J.
Cancer cell-autonomous contribution of type I interferon signaling to the efficacy of chemotherapy 1-gen-2014 Sistigu, A; Yamazaki, T; Vacchelli, E; Chaba, K; Enot, Dp; Adam, J; Vitale, I; Goubar, A; Baracco, Ee; Remédios, C; Fend, L; Hannani, D; Aymeric, L; Ma, Y; Niso Santano, M; Kepp, O; Schultze, Jl; Tüting, T; Belardelli, F; Bracci, L; La Sorsa, V; Ziccheddu, G; Sestili, P; Urbani, F; Delorenzi, M; Lacroix Triki, M; Quidville, V; Conforti, R; Spano, Jp; Pusztai, L; Poirier Colame, V; Delaloge, S; Penault Llorca, F; Ladoire, S; Arnould, L; Cyrta, J; Dessoliers, Mc; Eggermont, A; Bianchi, MARCO EMILIO; Pittet, M; Engblom, C; Pfirschke, C; Préville, X; Uzè, G; Schreiber, Rd; Chow, Mt; Smyth, Mj; Proietti, E; André, F; Kroemer, G; Zitvogel, L.
CCR2 polymorphism and nonprogressive HIV disease 1-gen-1998 Rizzardi, G. P.; Morawetz, R. A.; Vicenzi, E.; Ghezzi, S.; Poli, Guido; Lazzarin, A.; PANTALEO G., FOR THE SWISS HIV COHORT
Characterization of pancreatic NMDA receptors as possible drug targets for diabetes treatment 1-gen-2015 Marquard, Jan; Otter, Silke; Welters, Alena; Stirban, Alin; Fischer, Annelie; Eglinger, Jan; Herebian, Diran; Kletke, Olaf; Klemen, MaÅ¡a Skelin; Stoå¾er, Andraå; Wnendt, Stephan; Piemonti, Lorenzo; Kã¶hler, Martin; Ferrer, Jorge; Thorens, Bernard; Schliess, Freimut; Rupnik, Marjan Slak; Heise, Tim; Berggren, Per Olof; Klã¶cker, Nikolaj; Meissner, Thomas; Mayatepek, Ertan; Eberhard, Daniel; Kragl, Martin; Lammert, Eckhard
Coexpression of CD49b and LAG-3 identifies human and mouse T regulatory type 1 cells 1-gen-2013 Gagliani, N; Magnani, Cf; Huber, S; Gianolini, Me; Pala, M; Licona Limon, P; Guo, B; Herbert, Dr; Bulfone, A; Trentini, F; DI SERIO, Mariaclelia; Bacchetta, R; Andreani, M; Brockmann, L; Gregori, S; Flavell, Ra; Roncarolo, MARIA GRAZIA
Common noncoding UMOD promoter variants induce salt-sensitive hypertension and kidney damage by increasing uromodulin expression 1-gen-2013 Trudu, M; Janas, S; Lanzani, C; Debaix, H; Schaeffer, C; Ikehata, M; Citterio, L; Demaretz, S; Trevisani, F; Ristagno, G; Glaudemans, B; Laghmanik, ; Dell’Antonio, G; the Swiss Kidney Project on Genes in Hypertension team, 11; Loffing, J; Rastaldi, Mg; Manunta, Paolo; Devuyst, O; Rampolli, L.; Rampoldi, Luca
Comprehensive genomic access to vector integration in clinical gene therapy 1-gen-2009 Gabriel, R; Eckenberg, R; Paruzynski, A; Bartholomae, Cc; Nowrouzi, A; Arens, A; Howe, Sj; Recchia, A; Cattoglio, C; Wang, W; Faber, K; Schwarzwaelder, K; Kirsten, R; Deichmann, A; Ball, Cr; Balaggan, Ks; Yáñez Muñoz, Rj; Ali, Rr; Gaspar, Hb; Biasco, L; Aiuti, Alessandro; Cesana, D; Montini, E; Naldini, Luigi; Cohen Haguenauer, O; Mavilio, F; Thrasher, Aj; Glimm, H; von Kalle, C; Saurin, W; Schmidt, M.
Correction of junctional epidermolysis bullosa by transplantation of genetically modified epidermal stem cells 1-gen-2006 Mavilio, F; Pellegrini, G; Ferrari, S; Di Nunzio, F; Di Iorio, E; Recchia, A; Maruggi, G; Ferrari, Giuliana; Provasi, E; Bonini, MARIA CHIARA; Capurro, S; Conti, A; Magnoni, C; Giannetti, A; De Luca, M.
Dynamics of genetically engineered hematopoietic stem and progenitor cells after autologous transplantation in humans 1-gen-2018 Scala, S.; Basso-Ricci, L.; Dionisio, F.; Pellin, D.; Giannelli, S.; Salerio, F. A.; Leonardelli, L.; Cicalese, M. P.; Ferrua, F.; Aiuti, A.; Biasco, L.
Early treatment of COVID-19 with anakinra guided by soluble urokinase plasminogen receptor plasma levels: a double-blind, randomized controlled phase 3 trial 1-gen-2021 Kyriazopoulou, E.; Poulakou, G.; Milionis, H.; Metallidis, S.; Adamis, G.; Tsiakos, K.; Fragkou, A.; Rapti, A.; Damoulari, C.; Fantoni, M.; Kalomenidis, I.; Chrysos, G.; Angheben, A.; Kainis, I.; Alexiou, Z.; Castelli, F.; Serino, F. S.; Tsilika, M.; Bakakos, P.; Nicastri, E.; Tzavara, V.; Kostis, E.; Dagna, L.; Koufargyris, P.; Dimakou, K.; Savvanis, S.; Tzatzagou, G.; Chini, M.; Cavalli, Giulio.; Bassetti, M.; Katrini, K.; Kotsis, V.; Tsoukalas, G.; Selmi, C.; Bliziotis, I.; Samarkos, M.; Doumas, M.; Ktena, S.; Masgala, A.; Papanikolaou, I.; Kosmidou, M.; Myrodia, D. -M.; Argyraki, A.; Cardellino, C. S.; Koliakou, K.; Katsigianni, E. -I.; Rapti, V.; Giannitsioti, E.; Cingolani, A.; Micha, S.; Akinosoglou, K.; Liatsis-Douvitsas, O.; Symbardi, S.; Gatselis, N.; Mouktaroudi, M.; Ippolito, G.; Florou, E.; Kotsaki, A.; Netea, M. G.; Eugen-Olsen, J.; Kyprianou, M.; Panagopoulos, P.; Dalekos, G. N.; Giamarellos-Bourboulis, E. J.
Editing T cell specificity towards leukemia by zinc finger nucleases and lentiviral gene transfer 1-gen-2012 Provasi, E; Genovese, P; Lombardo, ANGELO LEONE; Magnani, Z; Liu Pei, Q; Reik, A; Chu, V; Paschon, D. E.; Zhang, L; Kuball, J; Camisa, B; Bondanza, Attilio; Casorati, G; Ponzoni, Maurilio; Ciceri, Fabio; Bordignon, Claudio; Greenberg, P. D.; Holmes, Mc; Gregory, Pd; Naldini, Luigi; Bonini, MARIA CHIARA
Endogenous microRNA Regulation Suppresses Transgene Expression in Hematopoietic Lineages and Enables Stable Gene Transfer 1-gen-2006 D, Brown B.; Venneri M., A.; Zingale, A; Nulll, nullSergi Sergi; Naldini, Luigi
Ensuring a future for gene therapy for rare diseases 1-gen-2022 Aiuti, A.; Pasinelli, F.; Naldini, L.
Epithelial calcineurin controls microbiota-dependent intestinal tumor development 1-gen-2016 Peuker, K; Muff, S; Wang, J; Künzel, S; Bosse, E; Zeissig, Y; Luzzi, G; Basic, M; Strigli, A; Ulbricht, A; Kaser, A; Arlt, A; Chavakis, T; van den Brink, Gr; Schafmayer, C; Egberts, J. H.; Becker, T; Bianchi, MARCO EMILIO; Bleich, A; Röcken, C; Hampe, J; Schreiber, S; Baines, Jf; Blumberg, Rs; Zeissig, S.
Generation of primary antigen-specific human T- and B-cell responses in immunocompetent SCID-hu mice 1-gen-2000 Carballido, J. M.; Namikawa, R.; CARBALLIDO PERIG, N.; Antonenko, S.; Roncarolo, MARIA GRAZIA; DE VRIES, J. E.
Genome editing: a tool for research and therapy: Targeted genome editing hits the clinic 1-gen-2014 Lombardo, ANGELO LEONE; Naldini, Luigi
Has SARS-CoV-2 reached peak fitness? 1-gen-2021 Burioni, R.; Topol, E. J.
Mostrati risultati da 1 a 20 di 43
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