Up to 10.5 Years of Follow-Up in 17 Subjects Treated with Hematopoietic Stem and Progenitor Cell Lentiviral Gene Therapy for Wiskott-Aldrich Syndrome

Ferrua, F;Cicalese, MP;Giannelli, S;Galimberti, S;Cenciarelli, S;Barzaghi, F;Migliavacca, M;Bernardo, ME;Calbi, V;Tucci, F;Albertazzi, E;Salerio, F;Canarutto, D;Fraschetta, F;Jones, R;Dott, C;Rivat, C;Hawkins, S;Valsecchi, MG;Ciceri, F;Naldini, L;Aiuti, A

2022-01-01